US Sickle cell disease Drugs market is projected to grow from $xx Mn in 2023 to $xx Mn by 2030, registering a CAGR of xx% during the forecast period of 2023 - 2030. The market for Sickle cell disease Drugs is growing rapidly as a result of increasing prevalence of sickle cell disease , increasing investment for healthcare infrastructure, increase in the number of research and development activities, Support provided by governments of different countries, patient advocacy programmes and incentives provided by regulatory authorities. Global Blood Therapeutics, Novartis, Emmaus Life Sciences, Bluebird Bio, Teva Pharmaceutical Industries Ltd, Pfizer Inc., Mylan N.V., Merck & Co., Inc., Johnson & Johnson Private Limited, Bristol-Myers Squibb Company, AbbVie Inc are the key global market players operating in sickle cell disease Drugs market.
US Sickle Cell Disease Drugs Market is valued at around $1 Bn in 2022 and is projected to reach $2.24 Bn by 2030, exhibiting a CAGR of 10.6% during the forecast period 2023-2030.
Sickle cell disease (SCD) is a genetic blood disorder characterized by the presence of abnormal haemoglobin that causes red blood cells to become rigid and sickle-shaped. It happens due to a mutation on the sixth position of the beta chain of hemoglobin where glutamic acid amino acid gets converted into valine. Bone marrow transplantation is the only permanent cure for SCD, it is usually reserved for individuals under the age of 16 since bone marrow transplant risk in adults is too great. Symptomatic relief and palliative care are also done for this disease. Hydroxyurea and Endari are the only two licensed medicines available for this disease. Global Blood Therapeutics, Novartis, Emmaus Life Sciences, Bluebird Bio, Teva Pharmaceutical Industries Ltd, Pfizer Inc., Mylan N.V., Merck & Co., Inc., Johnson & Johnson Private Limited, Bristol-Myers Squibb Company, AbbVie Inc are the key global market players operating in sickle cell disease Drugs market.
Market Drivers
Increasing prevalence of sickle cell disease.
Increasing investment in healthcare infrastructure
Increase in the number of research and development activities, Support provided by governments of different countries
Patient advocacy programmes and incentives provided by regulatory authorities like orphan drug designations. All these factors act as market growth drivers.
Market Restraints
High cost associated with treatment, lack of skilled professionals and physicians for treatment, lack of reimbursement policies and skilled professionals for treatment. All these act as restraints of sickle cell disease drug market development.
Notable deals in the Sickle cell disease Drugs market
In December 2021, Oxbryta (voxelotor) was approved by US FDA for treating sickle cell disease in patients aged 4 up to 11 years.
In May 2022, multiple daily doses of GBT601, Global Blood Therapeutics (GBT) experimental oral therapy for sickle cell disease (SCD), were well tolerated and showed promising pharmacological and efficacy signals in six patients in a phase I trial clinical trial.
Key players
Global Blood Therapeutics, Inc. Novartis AG Pfizer Inc. Bluebird Bio, Inc. Emmaus Life Sciences, Inc. Sanofi Genzyme Mast Therapeutics, Inc. Imara Inc. Vertex Pharmaceuticals Incorporated Global Blood Therapeutics, Inc.1. Executive Summary
1.1 Disease Overview
1.2 Global Scenario
1.3 Country Overview
1.4 Healthcare Scenario in Country
1.5 Patient Journey
1.6 Health Insurance Coverage in Country
1.7 Active Pharmaceutical Ingredient (API)
1.8 Recent Developments in the Country
2. Market Size and Forecasting
2.1 Epidemiology of Disease
2.2 Market Size (With Excel & Methodology)
2.3 Market Segmentation (Check all Segments in Segmentation Section)
3. Market Dynamics
3.1 Market Drivers
3.2 Market Restraints
4. Competitive Landscape
4.1 Major Market Share
4.2 Key Company Profile (Check all Companies in the Summary Section)
4.2.1 Company
4.2.1.1 Overview
4.2.1.2 Product Applications and Services
4.2.1.3 Recent Developments
4.2.1.4 Partnerships Ecosystem
4.2.1.5 Financials (Based on Availability)
5. Reimbursement Scenario
5.1 Reimbursement Regulation
5.2 Reimbursement Process for Diagnosis
5.3 Reimbursement Process for Treatment
6. Methodology and Scope
By Type
By Diagnosis
By Treatment
By Route of Administration
By End-Users
By Distribution Channel
Methodology for Database Creation
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