UK Adrenoleukodystrophy (ALD) Drugs Market Analysis

UK Adrenoleukodystrophy (ALD) Drugs Market Analysis


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UK Adrenoleukodystrophy (ALD) Drugs Market is projected to grow from $xx Mn in 2023 to $xx Mn by 2030, registering a CAGR of xx% during the forecast period of 2023 ? 2030. Drivers of acromegaly market are increasing cases of the disorder which in turn increased awareness and government focus motivated financial support to R&D. Poxel SA, Bluebird Bio Inc.,Viking Technologies, Minoryx Therapeutics sl., Apteeus SAS, Ashvattha Therapeutics LLC, NeuroVia Company, Autobahn Therapeutics Inc., Aldagen Inc., Celularity Inc., Imstem Biotechnology Inc., MedDay SA, and Orpheris Inc. are major competitors in the Global Adrenoleukodystrophy (ALD) drugs Market.

ID: IN10GBRD073 CATEGORY: Rare Diseases GEOGRAPHY: UK AUTHOR: Gaurav Bhongale

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UK Adrenoleukodystrophy (ALD) Drugs Market Analysis Summary

UK Adrenoleukodystrophy (ALD) Drugs Market is valued at around $0.01 Mn in 2022 and is projected to reach $0.03 Mn by 2030, exhibiting a CAGR of 13.9% during the forecast period 2023-2030.

An uncommon hereditary disorder called adrenoleukodystrophy leads to an accumulation of long-chain fatty acids (VLCFAs) in the brain. A mutation in the ABCD1 gene on the X chromosome causes ALD. The three adrenoleukodystrophies are Addison's disease, childhood cerebral ALD, and adrenomyelopathy. Between the ages of 3 and 10, cerebral ALD in children is known to advance quickly. The market for adrenoleukodystrophy treatments is expanding at an accelerated rate due to the rise in the frequency of chronic diseases worldwide. Drivers of the acromegaly market are increasing cases of the disorder which in turn increased awareness and government focus motivated financial support to R&D. Increased financial support for researchers working on innovative interventions as well as rising demand for tailored medications to treat the difficulties brought on by genetic mutations are driving the market's expansion. In addition, technological advancement, an increase in healthcare spending, and an increase in the occurrence of genetic disorders. Poxel SA, Bluebird Bio Inc., Viking Technologies, Minoryx Therapeutics sl., Apteeus SAS, Ashvattha Therapeutics LLC, NeuroVia Company, Autobahn Therapeutics Inc., Aldagen Inc., Celularity Inc., Imstem Biotechnology Inc., MedDay SA, and Orpheris Inc. are major competitors in the Global Adrenoleukodystrophy (ALD) Drugs Market.

Market Dynamics

Market Drivers

Drivers of the acromegaly market are increasing cases of the disorder which in turn increased awareness and government focus motivated financial support to R&D. Due to the global increase in the prevalence of chronic diseases, the market for treating adrenoleukodystrophy is growing quickly. One of the key factors fueling the growth of the market for adrenoleukodystrophy treatments is the rise in the number of infants suffering from the disorder globally. Increased financial support for researchers working on innovative interventions as well as rising demand for tailored medications to treat the difficulties brought on by genetic mutations are driving the market's expansion. The market is also impacted by the increase in research and development initiatives, mergers, and collaborations among manufacturers to treat ALD. In addition, technological advancement, an increase in healthcare spending, and an increase in the occurrence of genetic disorders.

Market Developments

The key targets in the Adrenoleukodystrophy pipeline products market are ATP Binding Cassette Sub Family D Member 1, Mitochondrial Pyruvate Carrier, Peroxisome Proliferator-Activated Receptor Gamma, Thyroid Hormone Receptor Beta, Acetyl CoA Carboxylase 1, Acetyl CoA Carboxylase 2, Adenosine Monophosphate Activated Protein Kinase (Hydroxymethylglutaryl) CoA Reductase, Cholinergic Receptor Nicotinic Subunit, IkappaB Kinase, Macrophage Colony Stimulating Factor 1 Receptor, and others. The key routes of administration in the Adrenoleukodystrophy pipeline products market are oral, intravenous, parenteral, intrathecal, intracerebral, and subcutaneous.

Key players

BioMarin Pharmaceutical Pfizer Novartis Sanofi Shire Takeda Pharmaceutical Company Astellas Pharma Ionis Pharmaceuticals Alnylam Pharmaceuticals Sangamo Therapeutics

1. Executive Summary
1.1 Disease Overview
1.2 Global Scenario
1.3 Country Overview
1.4 Healthcare Scenario in Country
1.5 Patient Journey
1.6 Health Insurance Coverage in Country
1.7 Active Pharmaceutical Ingredient (API)
1.8 Recent Developments in the Country

2. Market Size and Forecasting
2.1 Epidemiology of Disease
2.2 Market Size (With Excel & Methodology)
2.3 Market Segmentation (Check all Segments in Segmentation Section)

3. Market Dynamics
3.1 Market Drivers
3.2 Market Restraints

4. Competitive Landscape
4.1 Major Market Share

4.2 Key Company Profile (Check all Companies in the Summary Section)

4.2.1 Company
4.2.1.1 Overview
4.2.1.2 Product Applications and Services
4.2.1.3 Recent Developments
4.2.1.4 Partnerships Ecosystem
4.2.1.5 Financials (Based on Availability)

5. Reimbursement Scenario
5.1 Reimbursement Regulation
5.2 Reimbursement Process for Diagnosis
5.3 Reimbursement Process for Treatment

6. Methodology and Scope

Market Segmentations For UK Adrenoleukodystrophy (ALD) Drugs Market

By Route of Administration

  • Oral
  • IV
  • Parenteral
  • Intrathecal
  • Intracerebral
  • Subcutaneous

By Treatment

  • Adrenal gland treatment
  • Gene therapy oriented
  • Dietary supplements

By Diagnosis

  • Molecular genetic testing
  • Newborn screening
  • ACTH stimulation test
  • Magnetic resonance imaging (MRI)
  • Others

By Patient type

  • Paediatrics
  • Adult
  • Old age

By Distribution Channel

  • Hospitals
  • pharmacies

Methodology for Database Creation

Our database offers a comprehensive list of healthcare centers, meticulously curated to provide detailed information on a wide range of specialties and services. It includes top-tier hospitals, clinics, and diagnostic facilities across 30 countries and 24 specialties, ensuring users can find the healthcare services they need.​

Additionally, we provide a comprehensive list of Key Opinion Leaders (KOLs) based on your requirements. Our curated list captures various crucial aspects of the KOLs, offering more than just general information. Whether you're looking to boost brand awareness, drive engagement, or launch a new product, our extensive list of KOLs ensures you have the right experts by your side. Covering 30 countries and 36 specialties, our database guarantees access to the best KOLs in the healthcare industry, supporting strategic decisions and enhancing your initiatives.

How Do We Get It?

Our database is created and maintained through a combination of secondary and primary research methodologies.

1. Secondary Research

With many years of experience in the healthcare field, we have our own rich proprietary data from various past projects. This historical data serves as the foundation for our database. Our continuous process of gathering data involves:

  • Analyzing historical proprietary data collected from multiple projects.
  • Regularly updating our existing data sets with new findings and trends.
  • Ensuring data consistency and accuracy through rigorous validation processes.

With extensive experience in the field, we have developed a proprietary GenAI-based technology that is uniquely tailored to our organization. This advanced technology enables us to scan a wide array of relevant information sources across the internet. Our data-gathering process includes:

  • Searching through academic conferences, published research, citations, and social media platforms
  • Collecting and compiling diverse data to build a comprehensive and detailed database
  • Continuously updating our database with new information to ensure its relevance and accuracy

2. Primary Research

To complement and validate our secondary data, we engage in primary research through local tie-ups and partnerships. This process involves:

  • Collaborating with local healthcare providers, hospitals, and clinics to gather real-time data.
  • Conducting surveys, interviews, and field studies to collect fresh data directly from the source.
  • Continuously refreshing our database to ensure that the information remains current and reliable.
  • Validating secondary data through cross-referencing with primary data to ensure accuracy and relevance.

Combining Secondary and Primary Research

By integrating both secondary and primary research methodologies, we ensure that our database is comprehensive, accurate, and up-to-date. The combined process involves:

  • Merging historical data from secondary research with real-time data from primary research.
  • Conducting thorough data validation and cleansing to remove inconsistencies and errors.
  • Organizing data into a structured format that is easily accessible and usable for various applications.
  • Continuously monitoring and updating the database to reflect the latest developments and trends in the healthcare field.

Through this meticulous process, we create a final database tailored to each region and domain within the healthcare industry. This approach ensures that our clients receive reliable and relevant data, empowering them to make informed decisions and drive innovation in their respective fields.

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Last updated on: 04 July 2023
Updated by: Dr. Purav Gandhi

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