Egypt Fragile-X Syndrome Therapeutics Market is projected to grow from $xx Mn in 2023 to $xx Mn by 2030, registering a CAGR of xx% during the forecast period of 2023 - 2030. The most typical cause of inherited learning disabilities is fragile X syndrome (FXS), an X-linked genetic disorder. The global market is driven by the higher prevalence of males than females, the transmission of the disease from one generation to the next, and the rise in patients suffering from this and other genetic disorders. Aelis Farma Sas, Alcobra Ltd, Amo Pharma Limited, Confluence Pharmaceuticals Llc, F. Hoffmann-la Roche Ltd., Marinus Pharmaceuticals, Mi.to. Technology S.r.l., Neuren Pharmaceuticals Limited, Ovid Therapeutics Inc., Sage Therapeutics, Acadia Pharmaceuticals, Advanz Pharma Corp, Boehringer Ingelheim, GlaxoSmithKline, H. Lundbeck, Janssen, Novartis, Ots.
Egypt Fragile-X Syndrome Therapeutics Market is valued at around $70 thousand in 2022 and is projected to reach $134.45 thousand by 2030, exhibiting a CAGR of 8.5% during the forecast period 2023-2030.
The most typical cause of inherited learning disabilities is fragile X syndrome (FXS), an X-linked genetic disorder. The fragile X mental retardation 1 (FMR1) gene's 5' untranslated region has expanded CGG trinucleotide repeats, which are the root cause of FXS. The FMR1 gene is transcriptionally silenced as a result of this enlargement, which also causes the fragile X mental retardation protein (FMRP) to express less or not at all. FMRP has a key role in mediating synaptic plasticity and dendritic development.
A spectrum of behavioural and developmental problems, including poor eye contact, ADHD, anxiety, and other psychiatric and neurologic symptoms, are all part of the lifelong illness known as FXS (seizures and movement disorders). Other prevalent characteristics of the syndrome include physical characteristics including long faces, flat feet, and huge, prominent ears, as well as hearing brought on by the high recurrence of ear infections. The global market is driven by the higher prevalence of males than females, the transmission of the disease from one generation to the next, and the rise in patients suffering from this and other genetic disorders.
Aelis Farma Sas, Alcobra Ltd, Amo Pharma Limited, Confluence Pharmaceuticals Llc, F. Hoffmann-la Roche Ltd., Marinus Pharmaceuticals, Mi.to. Technology S.r.l., Neuren Pharmaceuticals Limited, Ovid Therapeutics Inc., Sage Therapeutics, Acadia Pharmaceuticals, Advanz Pharma Corp, Boehringer Ingelheim, GlaxoSmithKline, H. Lundbeck, Janssen, Novartis, Ots
Market Drivers
The global market is driven by the higher occurrences of males compared to females and the transmission of the disease from one generation to the next, which increases the number of patients with this and many other genetic disorders. The market is growing as a result of rising demand for specialised drugs to treat the problems caused by genetic abnormalities as well as increased financial assistance for researchers developing novel therapies. Increased research and development projects, mergers, and manufacturer cooperation to treat disease all have an effect on the market. Additionally, medical spending has increased, technology has advanced, and the prevalence of genetic illnesses has increased.
Market Development
The global market for this and many other genetic illnesses is driven by the higher occurrences of males relative to females and the transmission of the disease from one generation to the next. The market is growing due to rising demand for specialised pharmaceuticals to treat the problems caused by genetic abnormalities as well as increased financial assistance for researchers developing novel therapies. The rise in R&D projects, mergers, and manufacturer alliances to treat diseases all have an impact on the market. Additionally, medical spending has increased, technology has advanced, and genetic problems are becoming more common.
Key players
Ionis Pharmaceuticals Pfizer Wave Life Sciences Prothena Biosciences uniQure Voyager Therapeutics Stealth Biotherapeutics Neuren Pharmaceuticals Alcobra Alnylam Pharmaceuticals1. Executive Summary
1.1 Disease Overview
1.2 Global Scenario
1.3 Country Overview
1.4 Healthcare Scenario in Country
1.5 Patient Journey
1.6 Health Insurance Coverage in Country
1.7 Active Pharmaceutical Ingredient (API)
1.8 Recent Developments in the Country
2. Market Size and Forecasting
2.1 Epidemiology of Disease
2.2 Market Size (With Excel & Methodology)
2.3 Market Segmentation (Check all Segments in Segmentation Section)
3. Market Dynamics
3.1 Market Drivers
3.2 Market Restraints
4. Competitive Landscape
4.1 Major Market Share
4.2 Key Company Profile (Check all Companies in the Summary Section)
4.2.1 Company
4.2.1.1 Overview
4.2.1.2 Product Applications and Services
4.2.1.3 Recent Developments
4.2.1.4 Partnerships Ecosystem
4.2.1.5 Financials (Based on Availability)
5. Reimbursement Scenario
5.1 Reimbursement Regulation
5.2 Reimbursement Process for Diagnosis
5.3 Reimbursement Process for Treatment
6. Methodology and Scope
By Drug
By End User
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