China Oculopharyngeal Muscular Dystrophy (OPMD) market is projected to grow from $xx Mn in 2023 to $xx Mn by 2030, registering a CAGR of xx% during the forecast period of 2023 - 2030. The market for Oculopharyngeal Muscular Dystrophy (OPMD)is growing due to increase spending in research and development activities by pharmaceutical companies, incentives provided by regulatory authorities like orphan drug designations and accelerated approval pathways, patient support and advocacy programmes which help to increase awareness about disease and provide support to patients. Bristol-Myers Squibb, BioMarin, Sarepta Therapeutics, Benitec Biopharma Inc., Bioblast Pharma, PTC Therapeutics, NS Pharma, Nobelpharma Co., Ltd ,Santhera Pharmaceuticals, Pfizer Inc. ,Marathon Pharmaceuticals, Fibrogen, GSK are the key global market players.
China Oculopharyngeal Muscular Dystrophy (OPMD) Market is valued at around $96.46 Mn in 2022 and is projected to reach $193.62 Mn by 2030, exhibiting a CAGR of 9.1% during the forecast period 2023-2030.
An uncommon hereditary condition called oculopharyngeal muscular dystrophy (OPMD) damages the muscles of the eyes and throat. The quality of life of the patient may be impacted by the progressive nature of this condition, which frequently causes swallowing issues and eyelid drooping. Since OPMD currently has no known cure, treatment focuses on symptom management and improving the quality of life of affected individuals. To address swallowing and speech issues, treatment methods may include speech therapy and swallowing exercises. In some situations, surgical procedures to relieve symptoms, such as cricopharyngeal myotomy or eyelid surgery, may be considered. Gene therapies, small molecule drugs, and other novel treatment modalities aimed at targeting the underlying genetic mutations or disease mechanisms are also being developed. BB-301 (Pabparna) is under development for the treatment of dysphagia associated with oculopharyngeal muscular dystrophy, a type of congenital myopathy. The therapeutic candidate is administered through an intramuscular route. The therapeutic candidate is developed based on DNA-directed RNA interference (RNAi) technology that silences unwanted or disease-causing genes. Bristol-Myers Squibb, BioMarin, Sarepta Therapeutics, Benitec Biopharma Inc., Bioblast Pharma, PTC Therapeutics, NS Pharma, Nobelpharma Co., Ltd, Santhera Pharmaceuticals, Pfizer Inc., Marathon Pharmaceuticals, Fibrinogen, GSK are the key global market players.
Market Drivers
Research and development activities by pharmaceutical companies, incentives provided by regulatory authorities like orphan drug designations and accelerated approval pathways, patient support and advocacy programmes which help to increase awareness about the disease and provide support to patients all act as market growth drivers.
Market Restraints
Limited patient populations, difficulties in diagnosis and high costs associated with research and development all act as market growth restraints.
Key players
Sarepta Therapeutics Inc. Solid Biosciences Inc. Astellas Pharma Prometheus Therapeutics Inc. Sangamo Therapeutics Inc. Alnylam Pharmaceuticals Inc. Audentes Therapeutics Inc. Ultragenyx Pharmaceutical Inc. Shire PTC Therapeutics Inc.1. Executive Summary
1.1 Disease Overview
1.2 Global Scenario
1.3 Country Overview
1.4 Healthcare Scenario in Country
1.5 Patient Journey
1.6 Health Insurance Coverage in Country
1.7 Active Pharmaceutical Ingredient (API)
1.8 Recent Developments in the Country
2. Market Size and Forecasting
2.1 Epidemiology of Disease
2.2 Market Size (With Excel & Methodology)
2.3 Market Segmentation (Check all Segments in Segmentation Section)
3. Market Dynamics
3.1 Market Drivers
3.2 Market Restraints
4. Competitive Landscape
4.1 Major Market Share
4.2 Key Company Profile (Check all Companies in the Summary Section)
4.2.1 Company
4.2.1.1 Overview
4.2.1.2 Product Applications and Services
4.2.1.3 Recent Developments
4.2.1.4 Partnerships Ecosystem
4.2.1.5 Financials (Based on Availability)
5. Reimbursement Scenario
5.1 Reimbursement Regulation
5.2 Reimbursement Process for Diagnosis
5.3 Reimbursement Process for Treatment
6. Methodology and Scope
By Treatment
By Distribution Channels:
By end users
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