Brazil Morquio Syndrome (MPS-IV) Therapeutics Market is projected to grow from $xx Mn in 2023 to $xx Mn by 2030, registering a CAGR of xx% during the forecast period of 2023 ? 2030. As genetic illnesses like Morquio Syndrome (MPS-IV) has become more common, there is an increasing demand for specialised drugs to treat them. Major global players in Morquio Syndrome (MPS-IV) Therapeutics Market are BioMarin, Genzyme Corporation, Shire, JCR Pharmaceuticals Co., Ltd., Sanofi, Sangamo Therapeutics, ArmaGen and GREEN CROSS CORP, Concert Pharmaceuticals Inc., Alexion Pharmaceuticals Inc., and other players.
Brazil Morquio Syndrome (MPS-IV) Therapeutics Market is valued at around $0.002 Mn in 2022 and is projected to reach $0.01 Mn by 2030, exhibiting a CAGR of 10.5% during the forecast period 2023-2030.
Morquio Syndrome is a rare genetic metabolic disease or birth abnormality that mostly affects the skeleton. It is also known as MPS IV and mucopolysaccharidosis IV.
It is anticipated that the market for therapies for Morquio syndrome will expand quite quickly due to the rise in the number of products in the early and advanced stages of R&D as well as the emphasis on treating uncommon conditions. Many medicines that are now in the pipelines of various firms can be predicted to pass regulatory permission for marketing as a result of the recent approval of the drug elosulfase alpha (VIMIZIM), assuming they have positive clinical trial results. Major global players in Morquio Syndrome (MPS-IV) Therapeutics Market are BioMarin, Genzyme Corporation, Shire, JCR Pharmaceuticals Co., Ltd., Sanofi, Sangamo Therapeutics, ArmaGen and Green Cross Corp, Concert Pharmaceuticals Inc., Alexion Pharmaceuticals Inc., and other players.
Market Growth Drivers
Unmet clinical demands and improved treatment outcomes are major drivers of the increased demand for cutting-edge medications. Drugs like Elaprase and ALDURAZYME must cross the blood-brain barrier to be successful in treating the condition. The most severely affected patients with mucopolysaccharidosis (MPS) are unable to benefit from conventional therapy for their neurological symptoms and problems. For instance, the neurological symptoms of Hunter syndrome, which affect around two-thirds of all patients, are among the most incapacitating in those with the most severe symptoms. A sizeable fraction of the population still requires effective therapy because the neurological symptoms cannot be addressed by the available medications.
Market Restraints
High treatment costs are a defining feature of the Morquio syndrome treatment market. Enzyme replacement therapy is one of the pricey therapies for Morquio syndrome that not all patients may be able to afford. Some persons may have less access to care than others as a result of these issues.
Key players
uniQure Ionis Pharmaceuticals Alnylam Pharmaceuticals Pfizer Sanofi Shire plc BioMarin Pharmaceutical Inc. Orchard Therapeutics plc PTC Therapeutics Inc. Novartis1. Executive Summary
1.1 Disease Overview
1.2 Global Scenario
1.3 Country Overview
1.4 Healthcare Scenario in Country
1.5 Patient Journey
1.6 Health Insurance Coverage in Country
1.7 Active Pharmaceutical Ingredient (API)
1.8 Recent Developments in the Country
2. Market Size and Forecasting
2.1 Epidemiology of Disease
2.2 Market Size (With Excel & Methodology)
2.3 Market Segmentation (Check all Segments in Segmentation Section)
3. Market Dynamics
3.1 Market Drivers
3.2 Market Restraints
4. Competitive Landscape
4.1 Major Market Share
4.2 Key Company Profile (Check all Companies in the Summary Section)
4.2.1 Company
4.2.1.1 Overview
4.2.1.2 Product Applications and Services
4.2.1.3 Recent Developments
4.2.1.4 Partnerships Ecosystem
4.2.1.5 Financials (Based on Availability)
5. Reimbursement Scenario
5.1 Reimbursement Regulation
5.2 Reimbursement Process for Diagnosis
5.3 Reimbursement Process for Treatment
6. Methodology and Scope
By Treatment:
By Disease Type:
By Distribution Channels:
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