US Oculopharyngeal Muscular Dystrophy Market Analysis


  • Type: Rare Disease Area
  • Published : March 2021
  • Region: North America
  • Country: US
  • Report ID : 496

  • Format: PPT, PDF

US Oculopharyngeal Muscular Dystrophy (OPMD) Market – Growth, Trends, And Forecasts (2019 – 2028)


Report Overview

The US Oculopharyngeal Muscular Dystrophy (OPMD) drugs market size is USD xx billion in 2019 and projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

Oculopharyngeal Muscular Dystrophy treatment market is mainly containing various conventional drug therapies and novel gene therapies. Most of the novel therapies are under the product pipeline of major key players present in market. The US oculopharyngeal muscular dystrophy treatment Market is expected to experience steady growth over the forecast period due to rising prevalence in adult population. Rising awareness among people due public awareness programs conducted by government creating a lucrative opportunity for the key players present in Treatment Market. Increased demand for efficacious therapies among patients, rising investment on research and development activities by key players and introduction of novel disease therapies like RNA replacement strategy, mutation repression is anticipated to make Oculopharyngeal Muscular Dystrophy Treatment market highly competitive.

Market Drivers

Major driving factor involved in oculopharyngeal muscular dystrophy treatment market is increased prevalence in middle aged population. The conventional therapy mainly focused on symptomatic treatment and having lots of off target effects, this factor providing the additional opportunity for key players present in treatment market to expand their research and development activities and expected to drive the growth of market. Additionally, introduction of new disease-modifying and novel drugs therapies, increased drug development activities are expected to drive the treatment market. Furthermore, gene therapies such as mutation suppression, exon skipping are also anticipated to push the market during forecast period.

1. US Oculopharyngeal Muscular Dystrophy (OPMD) Market Overview……
A. Market Size
2. Market Growth Drivers…………………………………………………………………
A. Rise in US Prevalence of Oculopharyngeal Muscular Dystrophy (OPMD)
B. Growing R&D Investments and Reimbursement Policies
3. Major Oculopharyngeal Muscular Dystrophy (OPMD) types….……………
A. Autosomal dominant OPMD
B. Autosomal recessive OPMD
C. Others
4. Oculopharyngeal Muscular Dystrophy (OPMD) Market Segmentation…
A. Drug Class
I. Non-steroidal anti-inflammatory drugs (NSAIDs)
II. Corticosteroids
III. Others
B. Distribution Channel
I. Hospitals
II. Retail Pharmacies
III. Drug Stores
IV. Others
5. Oculopharyngeal Muscular Dystrophy (OPMD) Major Drugs Market……… 
A. Market Analysis, Insights and Forecast – By Drug Type
6. Competitive Landscape…………………………………………………………………
A. Major Players
B. Products in Pipeline
7. Key Company Profiles………………………………………………………………
A. Pfizer, overview, Product & Services, Strategies & Financials
B. Bioblast Pharma overview, Product & Services, Strategies & Financials
C. BioMarin, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape…………………………………
A. Policy changes and Reimbursement scenario
9. Factors Driving Future Growth………………………………………………………
A. New Trends and Development of Oculopharyngeal Muscular Dystrophy (OPMD) market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Drug Class:

Based on drug class, it is divided into non-steroidal anti-inflammatory drugs (NSAIDs), Corticosteroids and others.

By Disease Indication:

Based on disease indication, it is segmented into autosomal dominant OPMD, autosomal recessive OPMD and others.

By Distribution Channel:

Based on distribution channel, the Oculopharyngeal Muscular Dystrophy (OPMD) lowering drugs market has been segmented into hospital pharmacies, retail pharmacies, and online pharmacies. The retail pharmacies segment dominated the Oculopharyngeal Muscular Dystrophy (OPMD) lowering drugs market, in terms of revenue.

Top 5 Major Players

The US Oculopharyngeal Muscular Dystrophy (OPMD) market is highly competitive, and the prominent players in the market have adopted various strategies to garner maximum market share. Major players operating in the market include Bioblast Pharma, BioMarin, PTC Therapeutics, NS Pharma,Inc, and Pfizer Inc.

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision making for business stakeholders. Our focused approach to develop reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

Our analysis methodology involves three critical stages:

Stage I: Market Data Collection

Primary Interviews: We have developed a network of experts, freelancers and researchers across countries through which we engage with local experts to gather key data points and assumptions around each market. We also engage regularly with some of the best market research agencies such as Atheneum, GuidePoint, GLG, etc. to conduct surveys and interviews, and build intelligence. We have language translators as a part of our team, who between them can cover 30+ languages allowing us to extract better local insights.

Secondary Data Collection: We have developed strong expertise and experience in secondary data collection methods for developing unique data sets and research material. We gather data from multiple reliable sources to maintain the high level of accuracy and consistency. The market data is analysed and forecasted using appropriate statistical and coherent models. The report offers an overall analysis of the market size, growth, market share as well as segment-level analysis of the specific market. Our report includes precise, to the point information related to the overall market, competition, growth drivers, challenges, regulatory updates, and competition.

Data Sources: We have access to multiple highly reliable free and subscription data sources. We have many years of experience to understand which sources are more dependable for what and which to prefer for the reliable and latest information. The key sources of information include the following, but are not limited to:

  • Statistical Databases
  • Company Websites/Annual Reports
  • Trade Publications
  • Online Databases
  • Published Research Reports
  • Whitepapers
  • Press Releases of Key Market Players

Stage II: Market Data Analysis and Statistical Model

Market Trends: We generally look at macro parameter and micro indicators. The macro parameters includes changes in government policies, demand and supply of the market, government intervention programs and major market share. The micro indicators GDP growth, market size, market volume etc. We also understand nuances specific to each country like US, Canada, India, Germany, etc. and have worked across 60+ countries and hence no only understand global trends, but how these differ by country, how payment models, market structure, cultural parameters, etc. differ in each country.

Market Sizing and Analysis: Our expert data analytics team has created various market forecast models by employing the top-down approach i.e. start with large overall market and segment different areas and bottom-up approach i.e. start with population and epidemiology and roll up based on spend, etc., estimating the size of the market, and distributing among the geographic and/or product segments.

The top-down approach mainly used for new product forecasting and bottom-up approach is used for demand estimation of any product for different countries summed up to form total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

Data Triangulation & Validation:

Data triangulation of various sources and results of the research are carried out by benchmarking with reliable sources such as industry statistics, statistical databases and the company level averages etc.

We make sure to finalize the numbers in alignment to the market research. Firstly, our internal experts ensure thorough validation and checking to ensure the accurate and precise analysis and then validation is also done using multiple data analysis model.  Two level validation is done and entails finalization of report scope and to way of representation pattern.

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analysed and synthesized. A second series of interviews are done if necessary to check and validate. The future opportunities are analysed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results are then, interpreted by considering following parameters: (a partial list)

  • Establishing market drivers and trends
  • Analyzing regulatory landscape to understand future growth
  • Market Segment based analysis to obtain revenue / volume
  • Analyzing current needs and determining penetration to estimate market

Insights: Our reports deliver actionable insights backed with supporting facts and figures to assist you in achieving exemplary growth. Our in-depth analyses are interspersed with relevant insights and statistics to offer an executive-level view of a given market. The description helps in correlating many minor factors affecting the market and its impact to the different segments within the market.
Data curated from the analysis and interpretation are drawn to portray all in one consolidated report.

Presentation & Reporting: The market research report is presented in different forms such as charts by using a scientific approach for easy understanding. Historic, current and future analysis is provided for each market in terms of both value and volume. The size of the market is interpreted in the US Dollar value and the respective unit, based on the product, for volume consumptions.
The foreign exchange rates are calculated on the respective dates and for the respective regions covered in the study.

To request a free sample copy this report, please complete the form below.

    We value your inquiry and offer free customization with every report to fulfil your exact research needs.

    This website is secure and your personal details are safe.

    This report addresses

    • Market intelligence to enable effective decision making
    • Growth opportunities and trend analysis
    • Competitive benchmarking
    • Historical data & forecasts
    • Regional opportunities

    Need more?

    • Speak to our analyst to know how this research was put together
    • Add more countries or regions as part of customisation
    • Understand how this report can have direct impact on your revenue

    Get a custom report based on your requirements