UK Angelman Syndrome Market Analysis

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  • Type: Rare Disease Area
  • Published : April 2021
  • Region: Europe
  • Country: UK
  • Report ID : 2594

  • Format: PPT, PDF

UK Angelman Syndrome Therapeutics Market: Segmented by Therapeutics, and Distribution Channels – Size, Share, Impact, Growth, Trends, and Forecasts (2020 – 2028)

Published Date: June 2021

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SKU: 2594 Categories: ,

Report Overview

The UK Angelman Syndrome Therapeutics market size stood at around USD XX billion in 2020 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

The Angelman syndrome (AS) is a rare genetic and neurological disorder characterized by severe developmental delay and learning disabilities; absence or near absence of speech; inability to coordinate voluntary movements (ataxia); tremulousness with jerky movements of the arms and legs and a distinct behavioral pattern characterized by a happy disposition and unprovoked episodes of laughter and smiling. Angelman syndrome is caused by one of several different types of disruptions of a region of Chromosome 15, all involving a single gene, UBE3A. Although those with the syndrome may be unable to speak, many gradually learn to communicate through other means such as gesturing. Some children with Angelman syndrome may have distinctive facial features but most facial features reflect the normal parental traits.

The Angelman syndrome affects males and females in equal numbers. The prevalence of Angelman syndrome is estimated to be approximately 1 in 12,000-20,000 people in the whole population. However, many cases may go undiagnosed making it difficult to determine the disorder’s prevalence accurately. Angelman syndrome is not a degenerative disease. Children with Angelman syndrome can expect a normal lifespan.

Market Growth Drivers

The Angelman syndrome treatment market is expected to grow over the forecast period, due to increasing research activities and R&D expenditure. Government initiatives in developing new treatment options for Angelman syndrome are expected to drive the growth of the UK Angelman syndrome treatment market over the forecast period 2020-2028.

Furthermore, the effectiveness of the treatment by reducing the effect of the symptoms is also driving the UK Angelman syndrome treatment market growth. Improvements in the healthcare sector are further facilitating the growth of the Angelman syndrome treatment market over the forecast period.

Market Restraints

However, rising treatment costs, lack of awareness among patients and physicians & low diagnosis rate because of difficulty in diagnosis about Angelman Syndrome will be the major factors acting as restraints over the forecast period.

TABLE OF CONTENTS

1. UK Angelman Syndrome Therapeutics Market Overview……………………
A. Market Size
2. Market Growth Drivers & Restraints……………………………………….
Market Growth Drivers
A. Increasing Research Activities and R&D Activities
B. Government Initiatives in Developing New Treatment Options
C. Effectiveness of Treatments and Improvements in the Healthcare Sector
Market Restraints
A. High Treatment Costs
B. Low Diagnosis Rate
3. Major Types of Angelman Syndrome…………………………………………………
A. Genetic Angelman Syndrome
B. Acquired Angelman Syndrome
4. UK Angelman Syndrome Therapeutics Market Segmentation……………….
A. By Therapeutics
I. Anticonvulsants
II. Physical Therapy
III. Speech Therapy
IV. Occupational Therapy
V. Behavioural Modification Therapy
VI. Ankle Braces/ supports
VII. Special Communication Devices
VIII. Other Therapies
B. By Distribution Channel
I. Hospital Pharmacies
II. Retail Pharmacies
III. Online Pharmacies
5. UK Angelman Syndrome Major Products Market Share……………………
A. Market Analysis, Insights and Forecast – By Revenue Type
6. Competitive Landscape…………………………………………………………………
A. Major Players
B. Products in Pipeline
7. Key Company Profiles……………………………………………………………………
A. BioMarin Company overview, Product & Services, Strategies & Financials
B. Roche Company overview, Product & Services, Strategies & Financials
C. Ovid Company overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape……………………………
A. Policy changes and Reimbursement scenario
9. Factors Driving Future Growth…………………………………………………
A. New Trends and Development of Angelman Syndrome Therapeutics Market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Therapeutics:

In terms of therapeutics, the Angelman syndrome treatment market can be classified into

  • Anticonvulsants
  • Physical therapy
  • Speech therapy
  • Occupational therapy
  • Behavioural modification therapy
  • Ankle braces/supports
  • Special communication devices
  • Others

Anti-seizure medications are helpful to those experiencing seizures & usually seizures can be adequately controlled with a single medication. Most children with Angelman syndrome benefit from physical, speech and occupational therapy. Behavioural modification therapy may be used to discourage unwanted behaviours. Ankle braces/supports and physical therapy can help in the achievement of walking. Scoliosis can develop in about 10% of individuals and may require braces or surgical correction. The use of special communication devices such as computer picture-based systems, voice emitting devices and other modern uses of technology are also helping Angelman syndrome individuals provide for improved learning and social communication.

By Distribution Channel:

In terms of distribution channel, the Angelman syndrome treatment market has been segmented into

  • Hospital pharmacies
  • Retail pharmacies
  • Online pharmacies

The hospital segment has been accounted as the largest distribution channel in the past years. An increasing number of people are being hospitalized for Angelman Syndrome and the drugs for Angelman Syndrome are being sold on a large scale through hospitals. Therefore, hospital pharmacies are further anticipated to witness higher market growth during the forecast period.

Top 5 Major Players

The Angelman syndrome treatment market is a competitive one and the prominent players in the market have adopted various strategies to garner maximum market share. Various companies are focusing on organic growth strategies such as product launches, product approvals and others such as patents and events. On the other hand, the inorganic growth strategies such as acquisitions and partnership & collaborations. These activities have paved the way for the expansion of the business and the customer base of market players. Major players operating in the market include BioMarin Pharmaceuticals UK Ltd., Hoffmann-La-Roche Ltd, Ovid Therapeutics Inc, among others.

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision making for business stakeholders. Our focused approach to develop reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

Our analysis methodology involves three critical stages:

Stage I: Market Data Collection

Primary Interviews: We have developed a network of experts, freelancers and researchers across countries through which we engage with local experts to gather key data points and assumptions around each market. We also engage regularly with some of the best market research agencies such as Atheneum, GuidePoint, GLG, etc. to conduct surveys and interviews, and build intelligence. We have language translators as a part of our team, who between them can cover 30+ languages allowing us to extract better local insights.

Secondary Data Collection: We have developed strong expertise and experience in secondary data collection methods for developing unique data sets and research material. We gather data from multiple reliable sources to maintain the high level of accuracy and consistency. The market data is analysed and forecasted using appropriate statistical and coherent models. The report offers an overall analysis of the market size, growth, market share as well as segment-level analysis of the specific market. Our report includes precise, to the point information related to the overall market, competition, growth drivers, challenges, regulatory updates, and competition.

Data Sources: We have access to multiple highly reliable free and subscription data sources. We have many years of experience to understand which sources are more dependable for what and which to prefer for the reliable and latest information. The key sources of information include the following, but are not limited to:

  • Statistical Databases
  • Company Websites/Annual Reports
  • Trade Publications
  • Online Databases
  • Published Research Reports
  • Whitepapers
  • Press Releases of Key Market Players

Stage II: Market Data Analysis and Statistical Model

Market Trends: We generally look at macro parameter and micro indicators. The macro parameters includes changes in government policies, demand and supply of the market, government intervention programs and major market share. The micro indicators GDP growth, market size, market volume etc. We also understand nuances specific to each country like US, Canada, India, Germany, etc. and have worked across 60+ countries and hence no only understand global trends, but how these differ by country, how payment models, market structure, cultural parameters, etc. differ in each country.

Market Sizing and Analysis: Our expert data analytics team has created various market forecast models by employing the top-down approach i.e. start with large overall market and segment different areas and bottom-up approach i.e. start with population and epidemiology and roll up based on spend, etc., estimating the size of the market, and distributing among the geographic and/or product segments.

The top-down approach mainly used for new product forecasting and bottom-up approach is used for demand estimation of any product for different countries summed up to form total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

Data Triangulation & Validation:

Data triangulation of various sources and results of the research are carried out by benchmarking with reliable sources such as industry statistics, statistical databases and the company level averages etc.

We make sure to finalize the numbers in alignment to the market research. Firstly, our internal experts ensure thorough validation and checking to ensure the accurate and precise analysis and then validation is also done using multiple data analysis model.  Two level validation is done and entails finalization of report scope and to way of representation pattern.

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analysed and synthesized. A second series of interviews are done if necessary to check and validate. The future opportunities are analysed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results are then, interpreted by considering following parameters: (a partial list)

  • Establishing market drivers and trends
  • Analyzing regulatory landscape to understand future growth
  • Market Segment based analysis to obtain revenue / volume
  • Analyzing current needs and determining penetration to estimate market

Insights: Our reports deliver actionable insights backed with supporting facts and figures to assist you in achieving exemplary growth. Our in-depth analyses are interspersed with relevant insights and statistics to offer an executive-level view of a given market. The description helps in correlating many minor factors affecting the market and its impact to the different segments within the market.
Data curated from the analysis and interpretation are drawn to portray all in one consolidated report.

Presentation & Reporting: The market research report is presented in different forms such as charts by using a scientific approach for easy understanding. Historic, current and future analysis is provided for each market in terms of both value and volume. The size of the market is interpreted in the US Dollar value and the respective unit, based on the product, for volume consumptions.
The foreign exchange rates are calculated on the respective dates and for the respective regions covered in the study.

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