South Korea Pompe Disease Market Analysis


  • Type: Rare Disease Area
  • Published : June 2021
  • Region: Asia
  • Country: South Korea
  • Report ID : 4874

  • Format: PPT, PDF

South Korea Pompe Disease Market: Segmented By Therapy Type (Enzyme Replacement Therapy [ERT], Substrate Reduction Therapy [SRT], Gene Therapy and Others), By Route of Administration (Oral, Parenteral) and By Dosage Form (Solid, Liquid)- Growth, Trends and Forecasts (2019 – 2028)

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Report Overview

The South Korea Pompe Disease size stood at around USD xx billion in 2019 and is projected to reach xx billion by 2028, exhibiting a CAGR of around 2.8% during the forecast period.

Pompe disease is a progressive neuromuscular disease that shows signs of irreversible muscle damage and respiratory depression due to accumulation of sugar source in muscle cells because of deficiency or lack of lysosomal enzymes. This build-up occurs in organs and tissues, especially in muscles, causing them to break down. The additional glycogen builds up in the patient and is stored in skeletal muscle, heart, and other tissues, which causes the progressive indications of Pompe disease.

It is known to occurs infrequently, with an average of 1 out of 40,000 people, and the incidence frequency is very different according to race.

Market Drivers

The increase in the prevalence of Pompe disease is driving the Pompe disease market owing towards the increase of manufacturers focusing on expanding their pipeline to cater to the demand for Pompe disease treatment. Government has taken initiatives for developing and manufacturing innovative products for the diagnosis & treatment of Pompe disease is the other major factor driving growth of the Pompe Disease market.

Factor restraining the growth of the market is lack of cost-effective treatment. Available treatment options are very expensive, and lack of FDA approved drugs leads to the less affordability rate.


1. South Korea Pompe Disease Market Overview…………
A. Market Size
2. Market Growth Drivers………………………………………………….
A. Increase in Prevalence of Pompe Disease
B. Innovations in Diagnostics and Treatment
3. Types Of Pompe Disease………………………………..
A. Classic Infantile-Onset
B. Non-Classic Infantile-Onset
C. Late Onset
4. Pompe Disease Market Segmentation………………………….
A. Therapy Type
I. Enzyme Replacement Therapy (ERT)
II. Substrate Reduction Therapy (SRT)
III. Gene Therapy
IV. Others
B. Rout Of Administration
I. Oral
II. Parenteral
C. Dosage Form
I. Solid
II. Liquid
5. Pompe Disease Products Market Share………………………….
A. Market Analysis, Insights and Forecast – By Revenue
6. Competitive Landscape…………………………………………………………
A. Major Players
B. Products in Pipeline
7. Key Company Profiles……………………………………………………….
A. Pfizer Company Overview, Product & Services, Strategies & Financials
B. Merck Pharmaceuticals Company Overview, Product & Services, Strategies & Financials
C. Sanofi SA Corporation Company Overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape……………………………
A. Policy changes and Reimbursement scenario
9. Factors Driving Future Growth……………………………………………
A. New Trends and Development of Pompe Disease Market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Therapy Type:

On the basis of type of therapy, the Pompe disease market is segmented into enzyme replacement therapy (ERT), substrate reduction therapy (SRT), gene therapy and others.

Enzyme Replacement Therapy (ERT) segment dominated the Pompe Disease Market in terms of revenue in previous years. ERT is administered into the bloodstream and has been shown to reduce the abnormal thickening of the heart walls that is characteristic of Pompe disease. It also helps maintain muscle function and improve patients’ quality of life.

By Route of Administration:

According to route of administration market is segmented into oral and parenteral.

By Dosage Form:

According to dosage form market is segmented as solid and liquid.


Top Players

Product launches is the key strategy of the players in the Pompe disease industry.  Prominent players in market include Pfizer Inc., Alexion Pharmaceuticals Inc., Sanofi SA, Merck, Takeda Pharmaceuticals, AbbVie Inc.



Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision making for business stakeholders. Our focused approach to develop reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

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The top-down approach mainly used for new product forecasting and bottom-up approach is used for demand estimation of any product for different countries summed up to form total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

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We make sure to finalize the numbers in alignment to the market research. Firstly, our internal experts ensure thorough validation and checking to ensure the accurate and precise analysis and then validation is also done using multiple data analysis model.  Two level validation is done and entails finalization of report scope and to way of representation pattern.

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analysed and synthesized. A second series of interviews are done if necessary to check and validate. The future opportunities are analysed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results are then, interpreted by considering following parameters: (a partial list)

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