South Korea Mucopolysaccharidosis Treatment Market Analysis


  • Type: Rare Disease Area
  • Published : June 2021
  • Region: Asia
  • Country: South Korea
  • Report ID : 4966

  • Format: PPT, PDF

South Korea Mucopolysaccharidosis Treatment Market: Segmented By Treatment Type (Enzyme Replacement Therapy, Hematopoietic Stem Cell therapy [HSCT]) and By Route Of Administration (Intravenous and Intracerebroventricular [ICV])- Growth, Trends and Forecasts (2020 – 2028)


Report Overview

The South Korea Mucopolysaccharidosis treatment market size stood at around USD xx billion in 2020 and is projected to reach xx billion by 2028, exhibiting a CAGR of around xx% during the forecast period.

Mucopolysaccharidoses (MPSs) are a group of inherited metabolic diseases, which are a result of deficiencies in specific lysosomal enzymes that are required for the degradation of glycosaminoglycans (GAGs). It is known that there are eleven genes are causally related to MPS. Deficiency in a specific enzyme results in the accumulation of undegraded GAGs, which causes progressive damage to cells, tissues, and organs. MPS has a broad spectrum of clinical presentations with varied severity and prognosis for different types and individuals. MPS disorders are autosomal recessive, except for MPS II (Hunter syndrome), which has X‐linked inheritance and mainly affects males.

The prevalence of MPS in South Korea population is around 1.35 per 100,000. MPS II is the most prevalent type of MPS (54.6%), followed by MPS III (18.4%), MPS I (15.3%), MPS IV (9.5%), and MPS VI (1.4%).

Market Drivers

The lack of presence of wide range of therapeutics for the patients has led to the domination of enzyme replacement therapy. For instance, Elaprase is the most commonly and widely used drug for mucopolysaccharidosis type II (Hunter Syndrome). Expected launch of cheaper alternatives and advanced therapeutics is likely to drive the growth of South Korea’s MPS treatment market. There are a significant number of pipeline candidates for the development of advanced therapeutics for various types of MPS by global players, this will further propel the market drive. High cost of therapeutics along with poor diagnosis rates restrain the market growth.


1. South Korea Mucopolysaccharidosis Treatment Market Overview……..
A. Market Size
2. Market Growth Drivers……………………………………………….
A. Need for Advanced Therapeutics
B. Significant Number Of Pipeline Candidates
3. Types Of Mucopolysaccharidosis……………………………………….
A. Type I
B. Type II
C. Type III
D. Type IV
E. Type VI
F. Type VII
G. Type IX
4. Mucopolysaccharidosis Treatment Market Segmentation……………
A. Treatment Type
I. Enzyme Replacement Therapy
II. Hematopoietic Stem Cell therapy (HSCT)
B. Route Of Administration
I. Intravenous
II. Intracerebroventricular (ICV)
5. Mucopolysaccharidosis Treatment Market Share……………………………….
A. Market Analysis, Insights and Forecast – By Revenue
6. Competitive Landscape…………………………………………………………
A. Major Players
B. Products in Pipeline
7. Key Company Profiles……………………………………………….
A. BioMarin Company Overview, Product & Services, Strategies & Financials
B. Takeda Pharmaceuticals Korea Company Overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape…………………………
A. Policy changes and Reimbursement scenario
9. Factors Driving Future Growth……………………………………………
A. New Trends and Development of Mucopolysaccharidosis Treatment Market
B. Future Opportunities
10. Conclusion



Market Segmentation

By Treatment Type:

Hematopoietic stem cell transplantation (HSCT) and enzyme replacement therapy (ERT) are the main treatments for MPS disorders. HSCT is now the only therapy to prevent progressive neurodegenerative disorders in MPS I, II and VII. ERT is currently available for MPS I, II, IVA, VI, and VII, and it has been demonstrated to substantially reduce urinary GAG levels and significantly improve endurance, physiological activities, joint mobility, and quality of life. Additional therapies for MPS disorders are currently in clinical trials, and these include chaperone therapy, substrate reduction therapy, and gene therapy.

By Route of Administration:

According to route of administration market is segmented into intravenous and intracerebroventricular.

Top Players

Some of the key players operating in the MPS treatment market include Takeda Pharmaceutical, BioMarin Pharmaceuticals, Sarepta Therapeutics, GC Pharma, and others. Naglazyme (galsulfase) by BioMarin Pharmaceutical for the treatment of MPS type VI and Elaprase (idursulfase) by Takeda Pharmaceuticals for the treatment of MPS type II hold the monopoly in South Korea market.


Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

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The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

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