Indian Lysosomal Storage Disorders Treatment Market Analysis


  • Type: Rare Disease Area
  • Published : April 2021
  • Region: Asia
  • Country: India
  • Report ID : 1279

  • Format: PPT, PDF

Indian Lysosomal Storage Disease Treatment Market: Segmented By Therapy (Enzyme Replacement Therapy, Stem Cell Transplantation, Substrate Reduction Therapy, Others), By End-Users (Hospitals, Clinics, Stem Transplant Centers, Research Organizations, Others) – Growth, Trends, and Forecasts (2019 – 2028)

SKU: 1279 Categories: ,

Report Overview

The Indian Lysosomal Storage Disease Treatment market size stood at around USD XX Billion in 2019 and is projected to reach USD XX Billion by 2028, exhibiting a CAGR of XX% during the forecast period.

Lysosomal storage disease (LTD) is caused by defect in lysosomal functions and degradation pathway. It is caused by progressive accumulation of metabolites. LTD is a rare inherited metabolic disorder. There are 50 types of lysosomal storage diseases. Lysosomes are organelle present in eukaryotic cell. These consist of degradative enzymes enclosed in a membrane. Some of the lysosomal storage diseases are Fabry disease, Gaucher disease, glycogen storage disease II, Tay-Sachs disease, aspartylglucosaminuria, Batten disease, cystinosis, and others. Among them Gaucher disease is the most common type of lysosomal disorder which is characterized by neurological complication. Some of the symptoms such as fever, pain, numbness, tingling, or burning in the hands and feet, tiredness, red or purple skin sores, trouble in breathing, dizziness etc.

Market Drivers

Increase in incidence of lysosomal diseases, rise in diagnostic rate, surge in awareness about this rare disorder, increase in focus on research and development for diagnosis & drug development for treatment of lysosomal diseases, and implementation of orphan drug regulation that provides marketing and commercial benefits to pharmaceutical companies fuel the growth of the Indian lysosomal storage disease treatment market. However, high cost of available treatment, underdiagnosed lysosomal disorders because of heterogeneity of the rare lysosomal disorder, and decrease in efficiency of treatment option are likely to hamper the growth of the Indian lysosomal storage disease treatment market. Availability and advancement of chaperone and gene therapy is expected to propel the market during the forecast period.

1. Indian Lysosomal Storage Disease Treatment Market Overview……………
A. Market Size
2. Market Growth Drivers………………………………………………………………….
A. Increase in Incidence of Lysosomal Diseases
B. Increasing Research and Development for Diagnosis and Drug Development for Treatment of Lysosomal Diseases
3. Most Common Lysosomal Storage Disease………………………..……………
A. Gaucher Disease
B. Fabry Disease
C. Niemann- Pick Disease
D. Hunter Syndrome
E. Pompe Disease
4. Indian Lysosomal Storage Disease Treatment Market Segmentation……..
A. By Therapy
I. Enzyme Replacement Therapy
II. Stem Cell Transplantation
III. Substrate Reduction Therapy
IV. Others
B. By End-Users
I. Hospitals
II. Clinics
III. Stem Transplant Centers
IV. Research Organizations
V. Others
5. Lysosomal Storage Disease Treatment Major Products Market Share…
A. Key Findings
B. Market Analysis, Insights, and Forecast
6. Competitive Landscape…………………………………………………………………
A. Major Players
B. Products in Pipeline
7. Key Company Profiles…………………………………………………………………..
A. Shire Company overview, Product & Services, Strategies & Financials
B. Pfizer Company overview, Product & Services, Strategies & Financials
C. Sanofi Company overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape………………………………
A. Policy changes and Reimbursement scenario
9. Factors Driving Future Growth……………………………………………………
A. New Trends and Development of Lysosomal Storage Disease Treatment Market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Therapy:

Based on therapy, the Indian lysosomal storage disease treatment market can be categorized into enzyme replacement therapy, stem cell transplantation, substrate reduction therapy, and others. Enzyme replacement is the most preferred therapy for the treatment of lysosomal disorder. It is effective in reducing toxic storage material and organomegaly. Enzyme replacement therapy also helps in improving organ function in patients suffering from lysosomal disorder. Advanced research in stem cell transplantation has increased the success rate of treatment of lysosomal disease. Rise in the number of stem cell banks also fuels the growth of the Indian lysosomal storage disease treatment market.

By End-Users:

Based on end-user, the Indian lysosomal storage disease treatment market can be divided into hospitals, clinics, stem transplant centers, research organizations, and others. Hospitals was the leading segment of the Indian lysosomal storage disease treatment market in 2017. Research organizations are being funded by governments as well as pharmaceutical companies for the development of new treatment methods and drugs. Hence, the research organizations segment is expected to witness significant growth during the forecast period.

Major Players.

Increasing awareness regarding LSDs is expected to offer lucrative growth opportunities for players in the Indian lysosomal storage diseases therapeutics market.  Key players operating in the Indian lysosomal storage disease treatment market include Shire, Pfizer, Inc., Sanofi, BioMarin, Merck & Co., Inc., Actelion Pharmaceuticals Ltd., and Eli Lilly and Company.

Research Methodology

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  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

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The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

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