Indian Gaucher Disease Treatment Market Analysis


  • Type: Rare Disease Area
  • Published : April 2021
  • Region: Asia
  • Country: India
  • Report ID : 1281

  • Format: PPT, PDF

Indian Gaucher Disease Treatment Market: Segmented By Treatment (Enzyme Replacement Therapy (ERT), Substrate Reduction Treatment (SBT)), By Distribution Channel (Hospital Pharmacy, Retail Pharmacy & Others) – Growth, Trends, and Forecasts (2019 – 2028)

SKU: 1281 Categories: ,

Report Overview

Indian Gaucher Disease Treatment Market size stood at around USD XX billion in 2019 and is projected to reach USD XX billion by 2028, exhibiting a CAGR of XX% during the forecast period.

Gaucher Disease is an inherited disorder resulting build-up of certain fatty substance in certain organ, mainly in liver, bone marrow and spleen. It is the most common lysosomal storage disorders. Due to the low level of glucocerebrosidase an enzyme that breaks down the fatty chemical in the body known as glucocerebroside. Gaucher cells are normal scavenger cells known as macrophages that become full of unprocessed glucocerebroside. These unprocessed gaucher cells accumulate primarily in the sleep, liver and bone marrow and causes serious orang dysfunction and inflammation. Each pregnant female has a 1 in 4 chance that the baby will be born with the disease. Moreover, several pain reregulating therapies, blood transfusions, and orthopaedic surgery are used for Gaucher disease management. ERT helps in compensating the low levels of enzyme GBA, by providing Glucocerebrosidase into the Gaucher cells. Enzyme Replacement Therapy helps in providing relief from the symptoms associated with hematologic, visceral, and bone in the Gaucher disease patients.

Market Driving Factors

The Gaucher Disease Treatment Market is majorly driven by the factors such as increasing prevalence of this disease in all age men & women and subsequent increase in the number of drugs available in the market. Also, the rising number of investments by the key players and research institute for developing new drugs that act effectively in treating type II & type III Gaucher disease. Additionally, increasing government initiatives for creating awareness about Gaucher disease will also boost the Gaucher Disease market in the coming years. Gaucher disease causes massive clinical heterogeneity with symptoms of painless splenomegaly, anemia or thrombocytopenia, bone pain, chronic fatigue and pathologic fractures and also contributes to easy incidence of bruising and bleeding through the nose. Initially, Gaucher disease was treated in patients by the use of recombinant enzyme imiglucerase which was effective in retrograding the visceral and hematologic symptoms of the disease. With advancements in research and development, the scope for medicine with enhanced treating capabilities is growing significantly. Such factors are considered to promote significantly towards the growth of the Indian Gaucher disease treatment market.

1. Indian Gaucher Disease Treatment Market Overview……….…………………..
A. Market Size
2. Market Driving Factors…………………………………………….…….………….
A. Rising Prevalence of the Gaucher Disease
B. Increasing Government Initiatives for Creating Awareness
C. Advancements in Research & Development
3. Epidemiological Prevalence……………………………………………………….
A. Incidence Rate
B. Age-Specific
C. Prevalence Rate
4. Gaucher Disease Treatment Market Segmentation…………..………………….
A. By Treatment
a. Enzyme Replacement Therapy (ERT)
b. Substrate Reduction Treatment (SBT)
B. By Distribution Channel
a. Hospital Pharmacy
b. Retail Pharmacy
c. Others
5. Gaucher Disease Treatment Major Products Market Share…………………
A. Market Analysis, Insights and Forecast – By Revenue
6. Competitive Landscape…………………………………………………………………
A. Major Players
B. Products in Pipeline
7. Key Company Profiles………………………………………………………………….
A. Sanofi Company overview, Product & Services, Strategies & Financials
B. Takeda Pharmaceuticals Company overview, Product & Services, Strategies & Financials
C. Pfizer Company overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape…………………………………
A. Policy changes and Reimbursement scenario
9. Factors Driving Future Growth………………………………………………………
A. New Trends and Development of Gaucher Disease Treatment Market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Treatment:

Based on treatment type, the Gaucher disease treatment market is segmented as Enzyme Replacement Therapy (ERT), and Substrate Reduction Treatment (SBT). The ERT segment to hold dominating position in the market. This treatment market is primarily driven by its increased adoption across the globe for treating Gaucher disease, and higher awareness for using ERT.

By Distribution Channel:

On the basis of distribution channel, Gaucher disease market has also been segmented into hospital pharmacy, retail pharmacy & others. Hospital Pharmacy is dominating segment, with XX% of the growth rate in India.

Major Players

The market players are considerably contributing to the market growth by the adoption of various strategies including new product launch, merger, and acquisition, collaborations with government, and technological advancements to stay competitive in the market. The leading companies operating in the Gaucher Disease Treatment market include Sanofi (Genzyme Corporation), Pfizer Inc., Acetelion Pharmaceutical (J&J Ltd.), Shire Human Genetics Therapies, Inc., Takeda Pharmaceutical and JCR Pharmaceuticals Co Ltd. For Example, Takeda, a biopharmaceutical company has launched an Enzyme Replacement Therapy portfolio for lysosomal storage disorders (LSD) in India in line with its commitment to address the unmet needs of the patients living with rare diseases in India.

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision making for business stakeholders. Our focused approach to develop reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

Our analysis methodology involves three critical stages:

Stage I: Market Data Collection

Primary Interviews: We have developed a network of experts, freelancers and researchers across countries through which we engage with local experts to gather key data points and assumptions around each market. We also engage regularly with some of the best market research agencies such as Atheneum, GuidePoint, GLG, etc. to conduct surveys and interviews, and build intelligence. We have language translators as a part of our team, who between them can cover 30+ languages allowing us to extract better local insights.

Secondary Data Collection: We have developed strong expertise and experience in secondary data collection methods for developing unique data sets and research material. We gather data from multiple reliable sources to maintain the high level of accuracy and consistency. The market data is analysed and forecasted using appropriate statistical and coherent models. The report offers an overall analysis of the market size, growth, market share as well as segment-level analysis of the specific market. Our report includes precise, to the point information related to the overall market, competition, growth drivers, challenges, regulatory updates, and competition.

Data Sources: We have access to multiple highly reliable free and subscription data sources. We have many years of experience to understand which sources are more dependable for what and which to prefer for the reliable and latest information. The key sources of information include the following, but are not limited to:

  • Statistical Databases
  • Company Websites/Annual Reports
  • Trade Publications
  • Online Databases
  • Published Research Reports
  • Whitepapers
  • Press Releases of Key Market Players

Stage II: Market Data Analysis and Statistical Model

Market Trends: We generally look at macro parameter and micro indicators. The macro parameters includes changes in government policies, demand and supply of the market, government intervention programs and major market share. The micro indicators GDP growth, market size, market volume etc. We also understand nuances specific to each country like US, Canada, India, Germany, etc. and have worked across 60+ countries and hence no only understand global trends, but how these differ by country, how payment models, market structure, cultural parameters, etc. differ in each country.

Market Sizing and Analysis: Our expert data analytics team has created various market forecast models by employing the top-down approach i.e. start with large overall market and segment different areas and bottom-up approach i.e. start with population and epidemiology and roll up based on spend, etc., estimating the size of the market, and distributing among the geographic and/or product segments.

The top-down approach mainly used for new product forecasting and bottom-up approach is used for demand estimation of any product for different countries summed up to form total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

Data Triangulation & Validation:

Data triangulation of various sources and results of the research are carried out by benchmarking with reliable sources such as industry statistics, statistical databases and the company level averages etc.

We make sure to finalize the numbers in alignment to the market research. Firstly, our internal experts ensure thorough validation and checking to ensure the accurate and precise analysis and then validation is also done using multiple data analysis model.  Two level validation is done and entails finalization of report scope and to way of representation pattern.

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analysed and synthesized. A second series of interviews are done if necessary to check and validate. The future opportunities are analysed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results are then, interpreted by considering following parameters: (a partial list)

  • Establishing market drivers and trends
  • Analyzing regulatory landscape to understand future growth
  • Market Segment based analysis to obtain revenue / volume
  • Analyzing current needs and determining penetration to estimate market

Insights: Our reports deliver actionable insights backed with supporting facts and figures to assist you in achieving exemplary growth. Our in-depth analyses are interspersed with relevant insights and statistics to offer an executive-level view of a given market. The description helps in correlating many minor factors affecting the market and its impact to the different segments within the market.
Data curated from the analysis and interpretation are drawn to portray all in one consolidated report.

Presentation & Reporting: The market research report is presented in different forms such as charts by using a scientific approach for easy understanding. Historic, current and future analysis is provided for each market in terms of both value and volume. The size of the market is interpreted in the US Dollar value and the respective unit, based on the product, for volume consumptions.
The foreign exchange rates are calculated on the respective dates and for the respective regions covered in the study.

To request a free sample copy this report, please complete the form below.

    We value your inquiry and offer free customization with every report to fulfil your exact research needs.

    This website is secure and your personal details are safe.

    This report addresses

    • Market intelligence to enable effective decision making
    • Growth opportunities and trend analysis
    • Competitive benchmarking
    • Historical data & forecasts
    • Regional opportunities

    Need more?

    • Speak to our analyst to know how this research was put together
    • Add more countries or regions as part of customisation
    • Understand how this report can have direct impact on your revenue

    Get a custom report based on your requirements