Global Hunter Syndrome Treatment Market

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  • Type: Rare Disease Area
  • Published : March 2021
  • Region: Worldwide
  • Country: Other
  • Report ID : 123

  • Format: PPT, PDF

GLOBAL HUNTER SYNDROME (MUCOPOLYSACCHARIDOSIS II) DRUG MARKET – SIZE, SHARE, IMPACT, GROWTH, TRENDS, AND FORECASTS, GLOBAL, NORTH AMERICA, ASIA-PACIFIC, U.S. (2019 – 2028)

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Report Overview

The Global Hunter syndrome drugs market size stood at USD 0.94 billion in 2019 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

Hunter syndrome is a genetically inherited disease and caused due to a particular defect in the gene formation. The defect results in lack of production of major enzymes that enables a breakdown of sugary molecules in diet, termed as mucopolysaccharides. These get formed in the body of patient and leads into damage of vital organs. As a part of treatment, the patients are dosed with frequent replacements with enzymes that are responsible for synthesis of mucopolysaccharides to prevent their accumulation

Market Drivers                                                 

Increase in number of patients suffering from mucopolysaccharidosis II is likely to fuel the market growth during the forecast period. In addition, rise in the healthcare expenses and government initiatives for betterment of health. Increased R&D activities to counter hunter syndrome in children is more likely to propel the market demand during the forecast period

 

1. Global Hunter Syndrome Drugs Market Overview….…
A. Market Size
2. Market Growth Drivers…………………………………………
A. Rise in Global Prevalence of Hunter Syndrome
B. Growing R&D Investments and Reimbursement Policies
3. Major Treatments of Hunter Syndrome….………..………
A. Oral drugs
B. Therapies
C. Others
4. Hunter Syndrome Drugs Market Segmentation….………
A. Therapeutic types
I. Enzyme Replacement Therapy
II. Hematopoietic Stem Cell Transplant
III. Others
B. Geography
I. North America Market Analysis
II. Europe Market Analysis
III. Asia-Pacific Market Analysis
IV. Middle East and Africa Market Analysis
C. Distribution Channel
I. Hospital Pharmacies
II. Retail Pharmacies
III. Online Pharmacies
IV. Others
5. Hunter Syndrome Drugs Market Share…………..………….
A. Market Analysis, Insights and Forecast – By Revenue
6. Competitive Landscape…………………………….…
A. Major Players
B. Products in Pipeline
7. Key Company Profiles…………….………………………
A. BioMarin Pharmaceutical Inc. Product & Services, Strategies & Financials
B. Sanofi Company Product & Services, Strategies & Financials
C. Shire PLC Company, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape……………
A. Policy changes and Reimbursement scenario
9. Factors Driving Future Growth………………………………
A. New Trends and Development of Hunter Syndrome Drugs Market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Drug Class:

Based on treatment type, the market is categorized into enzyme replacement therapy (ERT), hematopoietic stem cell transplant (HSCT), and others. In 2018, the ERT segment accounted for the largest market share and is anticipated to hold onto its dominance over the forecast period. This is attributed to improved sales of Shire Plc’s ELAPRASE and potential for worldwide approval of GC Pharma’s product called Hunterase.

 

Shire Plc’s Elaprase (idursulfase) is the single major drug used for the treatment of Hunter syndrome, with GC Pharma’s Hunterase (idursulfase beta) being approved only in South Korea as of now. These drugs have addressed a significant unmet need. However, the high cost of these drugs is expected to be a major factor hindering their market growth. For instance, Idursulfase (Elaprase) drug costs around USD 3,100 per 6mg/3ml vial

By Distribution Channel:

Based on the distribution channel, the market has been segregated into hospitals, retail, online and other pharmacies

By Region:

The market can be segmented into North America, South America, Europe, Asia Pacific, Middle East and Africa. North America dominates the global market owing to presence of developed healthcare infrastructure and rising awareness among people. Asia Pacific market is likely to witness a faster growth owing to rapid developments in healthcare infrastructure and significant investments. Use of novel drugs to treat hunter syndrome and availability of drugs at affordable prices drives the regional market growth

Major Players

The key players in the hunter syndrome market are BioMarin Pharmaceutical Inc., Sangamo Therapeutics, Sanofi Company, JCR Pharmaceutical, GC Pharma, and Shrine Plc. Strategies such as product launches, R&D activities and collaborations are adopted by key players in order to expand their geographical presence and business portfolio

Currently, Shire Plc. (acquired by Takeda Pharmaceutical Company Limited in April 2019) is a prominent market player, with strong sales of its drug ELAPRASE, indicated for the treatment of Hunter syndrome. However, Shire plc is expected to face stiff competition from Green Cross (GC) Pharma over the forecast period. GC Pharma is emerging as a global player in the Hunter syndrome treatment market with its orphan drug, Hunterase

GC Pharma is undertaking inorganic growth strategies such as partnerships and collaborations for the commercialization and geographical expansion of Hunterase. For instance, in April 2019, Clinigen Group plc and GC Pharma entered into an exclusive licensing agreement under which Clinigen gained the rights to commercialize Hunterase in Japan

 

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision making for business stakeholders. Our focused approach to develop reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

Our analysis methodology involves three critical stages:

Stage I: Market Data Collection

Primary Interviews: We have developed a network of experts, freelancers and researchers across countries through which we engage with local experts to gather key data points and assumptions around each market. We also engage regularly with some of the best market research agencies such as Atheneum, GuidePoint, GLG, etc. to conduct surveys and interviews, and build intelligence. We have language translators as a part of our team, who between them can cover 30+ languages allowing us to extract better local insights.

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Stage II: Market Data Analysis and Statistical Model

Market Trends: We generally look at macro parameter and micro indicators. The macro parameters includes changes in government policies, demand and supply of the market, government intervention programs and major market share. The micro indicators GDP growth, market size, market volume etc. We also understand nuances specific to each country like US, Canada, India, Germany, etc. and have worked across 60+ countries and hence no only understand global trends, but how these differ by country, how payment models, market structure, cultural parameters, etc. differ in each country.

Market Sizing and Analysis: Our expert data analytics team has created various market forecast models by employing the top-down approach i.e. start with large overall market and segment different areas and bottom-up approach i.e. start with population and epidemiology and roll up based on spend, etc., estimating the size of the market, and distributing among the geographic and/or product segments.

The top-down approach mainly used for new product forecasting and bottom-up approach is used for demand estimation of any product for different countries summed up to form total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

Data Triangulation & Validation:

Data triangulation of various sources and results of the research are carried out by benchmarking with reliable sources such as industry statistics, statistical databases and the company level averages etc.

We make sure to finalize the numbers in alignment to the market research. Firstly, our internal experts ensure thorough validation and checking to ensure the accurate and precise analysis and then validation is also done using multiple data analysis model.  Two level validation is done and entails finalization of report scope and to way of representation pattern.

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analysed and synthesized. A second series of interviews are done if necessary to check and validate. The future opportunities are analysed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results are then, interpreted by considering following parameters: (a partial list)

  • Establishing market drivers and trends
  • Analyzing regulatory landscape to understand future growth
  • Market Segment based analysis to obtain revenue / volume
  • Analyzing current needs and determining penetration to estimate market

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Data curated from the analysis and interpretation are drawn to portray all in one consolidated report.

Presentation & Reporting: The market research report is presented in different forms such as charts by using a scientific approach for easy understanding. Historic, current and future analysis is provided for each market in terms of both value and volume. The size of the market is interpreted in the US Dollar value and the respective unit, based on the product, for volume consumptions.
The foreign exchange rates are calculated on the respective dates and for the respective regions covered in the study.

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