EU Gaucher Disease Treatment Market Analysis


  • Type: Rare Disease Area
  • Published : March 2021
  • Region: Europe
  • Country: Other
  • Report ID : 604

  • Format: PPT, PDF

EU Gaucher Disease Market, Market Segmented, by Disease Type (Type 1 Gaucher disease, Type 2 Gaucher Disease, and Type 3 Gaucher Disease), by Therapy type (Enzyme Replacement Therapy (ERT) and Substrate Reduction Therapy (SRT)), and by Distribution Channel (Hospitals, Retail Pharmacies, and Online Pharmacies)- Growth, Trends and Forecast, 2019-2028


Report Overview

The EU Gaucher Disease Treatment Market size stood at around USD xx billion in 2019 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period

Gaucher disease is an autosomal recessive inherited metabolism disorder where a type of fat (lipid) called glucocerebroside is unable to degrade. Body synthesis enzyme called glucocerebrosidase, which breakdowns and reprocesses glucocerebroside. Gaucher disease is caused by mutations of a single gene called GBA, which leads to very low levels of glucocerebrosidase enzyme leading to low degradation of glucocerebroside. There are three types of Gaucher disease namely: type 1, type 2, and type 3. Type 1 is the most common type of Gaucher disease while Type 2 and 3 are not as common as type 1

Market Drivers 

Approval of novel drugs is expected to boost growth of Gaucher disease treatment market.  Europe is expected to be the second largest market for Gaucher disease treatment due to the initiative taken by European organizations to spread awareness about Gaucher disease among the population. European Gaucher Alliance launched Gaucher Awareness Day aiming to spread awareness about this rare disease among the European population which will propel growth

1. EU Gaucher Disease Treatment Market Overview
A. Market Size
2. EU Gaucher Disease Treatment Market Growth Drivers and Restraints…
A. Aiming to spread awareness about this rare disease among the European population.
B. Approval of novel drugs
3. EU Gaucher Disease Treatment Market Segmentation………
A. By Disease Type
I. Type 1 Gaucher disease
II. Type 2 Gaucher Disease
III. Type 3 Gaucher Disease
B. By Therapy Type
I. Enzyme Replacement Therapy (ERT)
II. Substrate Reduction Therapy (SRT)
III. Hospitals
C. By Distribution Channel
I. Hospitals
II. Retail Pharmacies
III. Online Pharmacies
4. EU Gaucher Disease Treatment Major Market Share…
A. Market Analysis, Insights and Forecast by Revenue
5. Competitive Landscape…………………………………………………………
A. Major Players
B. Products in Pipeline
6. Key Company Profiles…………………………………………………………..
A. Johnson and Johnson, Company overview, Product & Services, Strategies & Financials
B. Pfizer, Inc, Company overview, Product & Services, Strategies & Financials
C. Shire Human Genetics Therapies, Inc., Company overview, Product & Services, Strategies & Financials
7. Healthcare Policies and Regulatory Landscape….………………………
A. Policy Changes and Reimbursement Scenario
8. Factors Driving Market Growth……………………………………………………
A. Key Industry Developments
B. Mergers and Acquisitions
9. Potential Growth Opportunities…………………………………………
A. Market Opportunities
B. Future Trends
10. Conclusion

Market Segmentation

By Disease Type

Based on the disease type, the market segmentation are, type 1 Gaucher disease, type 2 Gaucher disease, and type 3 Gaucher disease

Type 1 GD is the largest segment in the market. The condition does not affect the central nervous system (CNS), making it non neuronopathic in nature. This disorder can develop anytime between childhood and adulthood and the average life expectancy is 70 years

Type 2 and 3 are rare forms of this disease. Both these conditions are neuronopathic, causing CNS complications during the disease course. Infants with type 2 GD rarely survive beyond two years, due to lack of treatment and severity of disease progression

By Therapy type

Based on therapy type, the market  segmented are enzyme replacement therapy (ERT) and substrate reduction therapy (SRT)

ERT is commonly used for type 1 and type 3 to address issues unrelated to CNS as replacement enzymes cannot penetrate blood brain barrier. The treatment landscape is witnessing a gradual shift towards substrate replacement therapy (SRT)

By  Distribution Channel

Based on distribution channel, the market  segmented  are hospitals, retail pharmacies, and online pharmacies

Major Players 

Key players operating in Europe Gaucher disease treatment market include Genzyme Corporation, Pfizer, Inc., Shire Human Genetics Therapies, Inc., and  Johnson & Johnson

Genzyme’s Cerdelga receives European approval to treat Gaucher disease type 1. Sanofi subsidiary Genzyme has received marketing approval from European Commission (EC) for its Cerdelga (eliglustat) capsules to treat adult patients with Gaucher disease type1


Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision making for business stakeholders. Our focused approach to develop reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

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Market Sizing and Analysis: Our expert data analytics team has created various market forecast models by employing the top-down approach i.e. start with large overall market and segment different areas and bottom-up approach i.e. start with population and epidemiology and roll up based on spend, etc., estimating the size of the market, and distributing among the geographic and/or product segments.

The top-down approach mainly used for new product forecasting and bottom-up approach is used for demand estimation of any product for different countries summed up to form total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

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We make sure to finalize the numbers in alignment to the market research. Firstly, our internal experts ensure thorough validation and checking to ensure the accurate and precise analysis and then validation is also done using multiple data analysis model.  Two level validation is done and entails finalization of report scope and to way of representation pattern.

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analysed and synthesized. A second series of interviews are done if necessary to check and validate. The future opportunities are analysed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results are then, interpreted by considering following parameters: (a partial list)

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