China Rett Syndrome Therapeutics Market

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  • Type: Rare Disease Area
  • Published : April 2021
  • Region: Asia
  • Country: China
  • Report ID : 1610

  • Format: PPT, PDF

China Rett Syndrome Therapeutics Market: Segmented by Therapy (Occupational, Physical, Gene Therapy and Speech Therapy), Drug Type (Anti-Epileptics, Antidepressants, Proton Pump Inhibitors and Dietary Supplements) and Distribution Channels (Online, Hospital and Retail Pharmacies) – Size, Share, Growth, Trends, and Forecasts (2020 – 2028)

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Report Overview

China Rett Syndrome Therapeutics market size stood at around USD xx billion in 2020 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

Rett syndrome is a rare genetic neurological disorder that affects the brain development causing development disorders, loss of motor skills and speech, and it exclusively affects females. Only in rare cases are males affected. Globally classic Rett syndrome is the most common form of the disease, seen in 80-85 percent of all cases, with symptoms usually appearing between ages 6-18 months. The global incidence of Rett is estimated to be 1 in 10,000 female births.

Market Drivers

China is a growing market for Rett syndrome due to factors such as increase in incidence rate (1 in 10,000 female births across the globe). In addition to this the other factors that contribute to the growth of market are rise in healthcare expenditure, increase in awareness and rise in female population and increase in genetic mutations.

However, there are some restraining factors for the growth of Rett syndrome therapeutics market in China such as undiagnosed or misdiagnosed cases and determining the true frequency of these conditions in the general population is difficult.

1. China Rett Syndrome Therapeutics Market Overview……………………………………….
A. Market Size
2. Market Growth Drivers………………………………………………………………………
A. Rise in Female Population
B. Increase in Awareness
C. Increase in Genetic Mutations
D. Rise in Healthcare Expenditure
3. Types of Rett Syndrome…………………………………………………………………………….
A. Classic Rett Syndrome
B. Atypical Rett Syndrome
4. Rett Syndrome Therapeutics Market Segmentation……………………………………
A. By Therapy
I. Occupational Therapy
II. Physical Therapy
III. Gene Therapy
IV. Speech Therapy
B. By Drug Type
I. Anti-Epileptic Drugs
II. Antidepressants
III. Proton Pump Inhibitors
IV. Dietary Supplements
C. By Distribution Channels
I. Online Pharmacies
II. Hospital Pharmacies
III. Retail Pharmacies
5. Rett Syndrome Major Products Market Share………………………………………….
A. Market Analysis, Insights and Forecast – By Revenue Type
6. Competitive Landscape………………………………………………………………………
A. Major Players
B. Products in Pipeline
7. Key Company Profiles………………………………………………………………………
A. Novartis Company Overview, Product & Services, Strategies & Financials
B. BioShin Company Overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape……………………………………….
A. Policy Changes and Reimbursement Scenario
9. Factors Driving Future Growth……………………………………………………………
A. New Trends and Development of Rett Syndrome Therapeutics Market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Therapy:

On the basis of therapy, the China’s Rett syndrome therapeutics market can be segmented into occupational therapy, physical therapy, gene therapy and speech therapy.

Occupational therapy can improve the purposeful use of hands, and reduce repetitive hand and arm movements. Physical therapy can improve balance, flexibility, and walking skills. Speech therapy may improve speaking skills and teach patients nonverbal forms of communication and gene therapy- One approach to treating Rett syndrome is to use gene therapy to deliver a healthy copy of the MECP2 gene to the patient’s body.

By Drug Type:

On the basis of drug type, the China’s Rett syndrome therapeutics market can be segmented into anti-epileptic drugs, antidepressants, proton pump inhibitors and dietary supplements.

Anti-epileptic drugs can be used to help control seizure. Antidepressants can be used for the treatment of anxiety. Proton pump inhibitors can help reduce reflux and dietary supplements healthy diet can help improve growth and promote weight gain, some patients may need to be fed through a tube that directly connects to the stomach. Calcium and vitamin D supplementation can support bone health and reduce the risk of fractures.

By Distribution Channels:

On the basis of distribution channels, the China’s Rett syndrome therapeutics market can be segmented into online pharmacies, hospital and retail pharmacies. During the forecast period (2020-2028) hospital pharmacies segment generates the highest revenue due to most of the major products being prescription products, which are available in hospital pharmacies and a greater number of patients prefer to purchase the medicines from the hospital pharmacies. Retail pharmacies and online pharmacies are also growing due to the increasing number of outpatients and they prefer to purchase the medicines from these pharmacies.

Major Players

Some of the key players in China’s Rett syndrome therapeutics market are Novartis subsidiary- AveXis, Inc; Biohaven Pharmaceuticals; BioShin Limited.

Novartis pipeline drug- AVXS-201 is an investigational gene therapy developed by AveXis (now part of Novartis) for the treatment of Rett syndrome.

Biohaven Pharmaceuticals pipeline drug- Biohaven’s Bhv-5000 receives orphan drug designation from the FDA in Rett Syndrome. Biohaven Pharmaceuticals does not have direct presence in China but it has a subsidiary in China (BioShin Limited).

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

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The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

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