China Gaucher Disease Therapeutics Market

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  • Type: Rare Disease Area
  • Published : April 2021
  • Region: Asia
  • Country: China
  • Report ID : 1581

  • Format: PPT, PDF

China Gaucher Disease Therapeutics Market: Segmented by Therapy (Enzyme Replacement Therapy, Substrate Reduction Therapy), Surgery, Route of Administration (Oral, Parenteral), Distribution Channel (Hospital, Retail and Online Pharmacies)- Size, Share, Growth, Trends, and Forecasts (2019 – 2028)

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Report Overview

China Gaucher Disease Therapeutics market size stood at around USD xx billion in 2019 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of 4.7% during the forecast period.

Gaucher disease is a rare, inherited metabolic disorder in which deficiency of the enzyme glucocerebrosidase results in the accumulation of harmful quantities of certain fats (lipids), specifically the glycolipid glucocerebroside, throughout the body especially within the bone marrow, spleen and liver. The prevalence of Gaucher disease in China is about 1:200,000 to 1:500,000 persons. Incidence rate is 1.24 per 100,000 persons in China.

Market Drivers

China is a growing market for Gaucher disease due to factors such as increase in China’s incidence rate (1.24 per 100,000 persons) and prevalence rate (1:200,000 to 1:500,000 persons). Other factors that contribute to the growth of the market are awareness campaigns by various organizations and affordable reimbursement scenarios for treatment.

However, there are some restraining factors for growth of the Gaucher disease therapeutics market in China such as high cost of medicines, misdiagnosis (in 2019 61.9% of Gaucher disease patients have experienced misdiagnosis, and 27.9% of patients need 1-5 years to be diagnosed).

1. China Gaucher Disease Therapeutics Market Overview…………………………………..
A. Market Size
2. Market Growth Drivers………………………………………………………………………
A. Healthcare Reforms by Government
B. Increase in Awareness
C. Increase in Prevalence Rate
D. Affordable Reimbursement Scenario for Treatment
3. Types of Gaucher Disease ………………………………………………………………………..
A. Type I (Noncerebral Invenile)
B. Type II (Acute Neuronopathic)
C. Type III (chronic neuronopathic)
4. Gaucher Disease Therapeutics Market Segmentation…………………………………
A. By Therapy
I. Enzyme Replacement Therapy
II. Substrate Reduction Therapy
B. By Surgery
C. By Route of Administration
I. Oral
II. Parenteral
D. By Distribution Channels
I. Hospital Pharmacies
II. Retail Pharmacies
III. Online Pharmacies
5. Gaucher Disease Major Products Market Share……………………………………….
A. Market Analysis, Insights and Forecast – By Revenue Type
6. Competitive Landscape………………………………………………………………………
A. Major Players
B. Products in Pipeline
7. Key Company Profiles………………………………………………………………………
A. Takeda Company Overview, Product & Services, Strategies & Financials
B. Sanofi Company Overview, Product & Services, Strategies & Financials
C. Pharming Group Company Overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape……………………………………….
A. Policy Changes and Reimbursement Scenario
9. Factors Driving Future Growth……………………………………………………………
A. New Trends and Development of Gaucher Disease Therapeutics Market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Therapy:

On the basis of therapy, the China Gaucher disease therapeutics market can be segmented into enzyme replacement therapy and substrate reduction therapy.

Enzyme replacement therapy most commonly used for the treatment and it consists of Imiglucerase, Velaglucerase and others. Substrate reduction therapy consists of glucosylceramide synthase inhibitors such as Miglustat, Eliglustat.

By Surgery:

On the basis of surgery, the China Gaucher disease therapeutics market can be segmented into surgery. Surgery consists of spleen removal and bone marrow transplantation.

By Route of Administration:

On the basis of route of administration, the China Gaucher disease therapeutics market can be segmented into oral and parenteral. Oral route of administration is usually the preferred method due to its convenience and pain-free administration. Oral medication is associated with a better quality of life, compared with infusion therapy (parenteral route of administration).

By Distribution Channel:

On the basis of the distribution channel, the China Gaucher disease therapeutics market can be segmented into retail, online and hospital pharmacies. During the forecast period (2019-2028) online pharmacies and retail pharmacies will dominate the market due to easy availability of medicines at a less price compared to hospital pharmacies. Hospital pharmacies are the second largest distribution channels during the forecast period (2019-2028).

Major Players

Some of the key players in China Gaucher disease therapeutics market are Sanofi Genzyme; Takeda Pharmaceutical Company Limited; Pharming Group NV.

Key players are adopting various strategies such as partnership, awareness campaigns to increase the market share. For instance, Genzyme began donating Cerezyme free of charge to patients with severe Gaucher’s disease in China, as well as donating drugs for free, the manufacturer worked closely with the China Charity Federation (CCF) to increase public awareness of the disease and promote research into policy and insurance coverage for orphan diseases.

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision making for business stakeholders. Our focused approach to develop reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

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Market Sizing and Analysis: Our expert data analytics team has created various market forecast models by employing the top-down approach i.e. start with large overall market and segment different areas and bottom-up approach i.e. start with population and epidemiology and roll up based on spend, etc., estimating the size of the market, and distributing among the geographic and/or product segments.

The top-down approach mainly used for new product forecasting and bottom-up approach is used for demand estimation of any product for different countries summed up to form total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

Data Triangulation & Validation:

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We make sure to finalize the numbers in alignment to the market research. Firstly, our internal experts ensure thorough validation and checking to ensure the accurate and precise analysis and then validation is also done using multiple data analysis model.  Two level validation is done and entails finalization of report scope and to way of representation pattern.

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analysed and synthesized. A second series of interviews are done if necessary to check and validate. The future opportunities are analysed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results are then, interpreted by considering following parameters: (a partial list)

  • Establishing market drivers and trends
  • Analyzing regulatory landscape to understand future growth
  • Market Segment based analysis to obtain revenue / volume
  • Analyzing current needs and determining penetration to estimate market

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Data curated from the analysis and interpretation are drawn to portray all in one consolidated report.

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The foreign exchange rates are calculated on the respective dates and for the respective regions covered in the study.

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