China Cystic Fibrosis Therapeutics Market


  • Type: Rare Disease Area
  • Published : April 2021
  • Region: Asia
  • Country: China
  • Report ID : 1568

  • Format: PPT, PDF

China Cystic Fibrosis Therapeutics Market – Segmented by Drug Type (CFTR Modulators, Mucolytics, Bronchodilators, and Pancreatic Enzyme Supplements), Surgery (Lung Transplant and Liver Transplant), Route of Administration (Oral, Inhaled, Parenteral)- Size, Share, Growth, Trends, And Forecasts (2019 – 2028)

SKU: 1568 Categories: ,

Report Overview

The China Cystic Fibrosis Therapeutics market size stood at USD xx billion in 2019 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

The diagnosis and treatment of Cystic Fibrosis disease are an important public health issue and a challenge for medical care in China. The Incidence rate of Cystic Fibrosis disease in China is 1 person per 1,00,000. With its enormous population, increase in paediatric population (14.65 million in 2019) and economic inequalities, several mutations (1898+5G>T, c.2909G>A, 3068T>G) in cystic fibrosis disease in China faces considerable challenges in improving the standard of care for patients who are affected by cystic fibrosis disease. It is found that the median age of a patient who is affected by cystic fibrosis is 10.55 years old.

Market Drivers

China is the growing market for Cystic Fibrosis disease due to increasing paediatric population (14.65 million in 2019), increase in mutation of genes, rise in smoking rates (300 million smokers in 2019 and 180 million children are exposed to second-hand smoke at least once a day in typical week) results in increase in Prevalence rate. Advances in screening and treatment technologies will lead to increase in market growth of cystic fibrosis disease. The growing focus of companies towards product enhancement and clinical studies will foster the growth of the market.

There are some restraining factors for the growth of Cystic Fibrosis therapeutics market in China such as complex drug development process, expensive treatment options, under diagnosis, misdiagnosis and missed diagnosis.

1. China Cystic Fibrosis Therapeutics Market Overview……………………………………..
A. Market Size
2. Market Growth Drivers……………………………………………………………………….
A. Rise In Mutation of Genes, Increase in Prevalence
B. Rise In Smoking Rates
C. Advances In Screening and Treatment Technologies
D. Product Enhancement and Clinical Studies
3. Major Types of Cystic Fibrosis by Mutations ………………….……………………………
A. Class 1 (Defective Protein Production)
B. Class 2 (Defective Protein Processing)
C. Class 3 (Defective Regulation)
D. Class 4 (Defective Conduction)
E. Class 5 (Reduced Amounts of Functional CFTR Protein)
4. Cystic Fibrosis Therapeutics Market Segmentation……………………………………….
A. By Drug Type
I. CFTR Modulators
II. Mucolytics
III. Bronchodilators
IV. Pancreatic Enzyme Supplements
B. By Surgery
I. Lung Transplant
II. Liver Transplant
C. By Route of Administration
I. Oral
II. Inhaled
III. Parenteral
5. Cystic Fibrosis Major Products Market Share………………………………………….
A. Market Analysis, Insights and Forecast – By Revenue Type
6. Competitive Landscape…………………………….……………………………………….
A. Major Players
B. Products In Pipeline
7. Key Company Profiles…………….……………………………………….……………….
A. Vertex Company Product & Services, Strategies & Financials
B. Arcturus Company Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape…………………….…….……….…
A. New Policies and Reimbursement Scenario
9. Factors Driving Future Growth……………………………………………………………
A. New Trends and Development of Cystic Fibrosis Therapeutics Market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Drug Type:

On the basis of the drug type, the China Cystic Fibrosis therapeutics market is segmented into CFTR modulators, mucolytics, bronchodilators and pancreatic enzyme supplements.

CFTR modulators includes Ivacaftor and Lumacaftor. Mucolytics consists of Dornase Alfa, Hypertonic saline. Bronchodilator’s drug includes Albuterol and Levalbuterol. Pancreatic enzyme supplements include Lipase, Protease and Amylase.

By Surgery:

On the basis of the surgery, the China cystic fibrosis therapeutics market can be segmented into lung transplant and liver transplant. Lung transplant is used in case of severe breathing problems, life-threatening lung complications or increasing resistance to antibiotics for lung infections, lung transplantation may be an option. Liver transplant- For severe cystic fibrosis-related liver disease, such as cirrhosis, liver transplant may be an option.

By Route of administration:

Based on the route of administration, the China cystic fibrosis therapeutics market has been segmented into oral, inhaled and parenteral.

Oral route is most commonly used due to safe, simple, and convenient for administration of drugs.

Inhaled- Route of administration includes bronchodilators which may widen airways by helping the surrounding muscles relax, this could allow more air to travel through the airways, which may help other medications work more effectively.

Parenteral- In case of acute or emergency treatment of disease this route is preferred.

Major Players

Some of the key players in the Cystic Fibrosis therapeutics market are Actavis Pharma Inc; Vertex Pharmaceuticals LLC; Aridis Pharmaceuticals Inc; Arcturus Therapeutics Inc; Johnson & Johnson and others.

Key players are adopting various strategies such as strategic collaboration to increase their market share and also to develop new therapy for effective treatment of the disease. For instance, Arcturus Therapeutics announces strategic collaboration with Johnson and Johnson innovation to discover and develop RNA medicines. It also received up to 3 million dollars from cystic fibrosis foundation to advance a novel LUNAR formulated mRNA CFTR therapeutic.

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision making for business stakeholders. Our focused approach to develop reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

Our analysis methodology involves three critical stages:

Stage I: Market Data Collection

Primary Interviews: We have developed a network of experts, freelancers and researchers across countries through which we engage with local experts to gather key data points and assumptions around each market. We also engage regularly with some of the best market research agencies such as Atheneum, GuidePoint, GLG, etc. to conduct surveys and interviews, and build intelligence. We have language translators as a part of our team, who between them can cover 30+ languages allowing us to extract better local insights.

Secondary Data Collection: We have developed strong expertise and experience in secondary data collection methods for developing unique data sets and research material. We gather data from multiple reliable sources to maintain the high level of accuracy and consistency. The market data is analysed and forecasted using appropriate statistical and coherent models. The report offers an overall analysis of the market size, growth, market share as well as segment-level analysis of the specific market. Our report includes precise, to the point information related to the overall market, competition, growth drivers, challenges, regulatory updates, and competition.

Data Sources: We have access to multiple highly reliable free and subscription data sources. We have many years of experience to understand which sources are more dependable for what and which to prefer for the reliable and latest information. The key sources of information include the following, but are not limited to:

  • Statistical Databases
  • Company Websites/Annual Reports
  • Trade Publications
  • Online Databases
  • Published Research Reports
  • Whitepapers
  • Press Releases of Key Market Players

Stage II: Market Data Analysis and Statistical Model

Market Trends: We generally look at macro parameter and micro indicators. The macro parameters includes changes in government policies, demand and supply of the market, government intervention programs and major market share. The micro indicators GDP growth, market size, market volume etc. We also understand nuances specific to each country like US, Canada, India, Germany, etc. and have worked across 60+ countries and hence no only understand global trends, but how these differ by country, how payment models, market structure, cultural parameters, etc. differ in each country.

Market Sizing and Analysis: Our expert data analytics team has created various market forecast models by employing the top-down approach i.e. start with large overall market and segment different areas and bottom-up approach i.e. start with population and epidemiology and roll up based on spend, etc., estimating the size of the market, and distributing among the geographic and/or product segments.

The top-down approach mainly used for new product forecasting and bottom-up approach is used for demand estimation of any product for different countries summed up to form total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

Data Triangulation & Validation:

Data triangulation of various sources and results of the research are carried out by benchmarking with reliable sources such as industry statistics, statistical databases and the company level averages etc.

We make sure to finalize the numbers in alignment to the market research. Firstly, our internal experts ensure thorough validation and checking to ensure the accurate and precise analysis and then validation is also done using multiple data analysis model.  Two level validation is done and entails finalization of report scope and to way of representation pattern.

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analysed and synthesized. A second series of interviews are done if necessary to check and validate. The future opportunities are analysed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results are then, interpreted by considering following parameters: (a partial list)

  • Establishing market drivers and trends
  • Analyzing regulatory landscape to understand future growth
  • Market Segment based analysis to obtain revenue / volume
  • Analyzing current needs and determining penetration to estimate market

Insights: Our reports deliver actionable insights backed with supporting facts and figures to assist you in achieving exemplary growth. Our in-depth analyses are interspersed with relevant insights and statistics to offer an executive-level view of a given market. The description helps in correlating many minor factors affecting the market and its impact to the different segments within the market.
Data curated from the analysis and interpretation are drawn to portray all in one consolidated report.

Presentation & Reporting: The market research report is presented in different forms such as charts by using a scientific approach for easy understanding. Historic, current and future analysis is provided for each market in terms of both value and volume. The size of the market is interpreted in the US Dollar value and the respective unit, based on the product, for volume consumptions.
The foreign exchange rates are calculated on the respective dates and for the respective regions covered in the study.

To request a free sample copy this report, please complete the form below.

    We value your inquiry and offer free customization with every report to fulfil your exact research needs.

    This website is secure and your personal details are safe.

    This report addresses

    • Market intelligence to enable effective decision making
    • Growth opportunities and trend analysis
    • Competitive benchmarking
    • Historical data & forecasts
    • Regional opportunities

    Need more?

    • Speak to our analyst to know how this research was put together
    • Add more countries or regions as part of customisation
    • Understand how this report can have direct impact on your revenue

    Get a custom report based on your requirements