China Charcot-Marie-Tooth Disease (CMT) Therapeutics Market


  • Type: Rare Disease Area
  • Published : April 2021
  • Region: Asia
  • Country: China
  • Report ID : 1611

  • Format: PPT, PDF

China Charcot-Marie-Tooth Disease (CMT) Therapeutics Market: Segmented by Therapy (Supportive Therapy), Surgery, Disease Type (CMT-1, CMT-2, CMT-3, CMT-4 and CMTX1)- Size, Share, Growth, Trends, and Forecasts (2020 – 2028)

SKU: 1611 Categories: ,

Report Overview

China Charcot-Marie-Tooth disease (CMT) Therapeutics market size stood at around USD xx billion in 2020 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

Charcot-Marie-Tooth (CMT) disease is a group of disorders in which the motor and/or sensory peripheral nerves are affected, resulting in muscle weakness and atrophy, as well as sensory loss. These manifestations occur first in the distal legs and later in the hands. In China the overall incidence of CMT is about 40/100,000.

Market Drivers

China is a growing market for Charcot-Marie-Tooth disease (CMT) due to factors such as increase in China’s incidence rate (40/100,000). In addition to this, other factors that contribute to the growth of the market are increase in genetic disorders and increased focus towards targeted therapies.

However, there are some restraining factors for growth of Charcot-Marie-Tooth disease (CMT) therapeutics market in China such high cost of treatment.

1. China Charcot-Marie-Tooth Disease (CMT) Therapeutics Market Overview..
A. Market Size
2. Market Growth Drivers……………………………………………………………………………………..
A. Increase in Incidence Rate
B. Increase in Genetic Disorders
C. Increased Focus Towards Targeted Therapies
3. Types of Charcot-Marie-Tooth Disease (CMT) by Nerve Conduction Velocity..
A. Axonal Type
B. Myelin Type
4. Charcot-Marie-Tooth Disease (CMT) Therapeutics Market Segmentation….
A. By Therapy
I. Supportive Therapy
B. By Surgery
C. By Disease Type
I. CMT-1
5. Charcot-Marie-Tooth Disease (CMT) Major Products Market Share……….
A. Market Analysis, Insights and Forecast – By Revenue Type
6. Competitive Landscape……………………………………………………………………………………..
A. Major Players
B. Products in Pipeline
7. Key Company Profiles………………………………………………………………………………………..
A. Pharnext Company Overview, Product & Services, Strategies & Financials
B. Tasly Pharmaceutical Company Overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape……………………………………………
A. Policy Changes and Reimbursement Scenario
9. Factors Driving Future Growth…………………………………………………………………………
A. New Trends and Development of Charcot-Marie-Tooth Disease (CMT) Therapeutics Market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Therapy:

On the basis of therapy, China’s Charcot-Marie-Tooth disease (CMT) therapeutics market can be segmented into supportive therapy.

Appropriate supportive therapy can significantly improve the quality of life of patients. Supportive therapy includes rehabilitation treatment, avoiding the drugs that may aggravate the CMT such as Vincristine, Amiodarone, Metronidazole and Dapsone.

By Surgery:

Most patients who have moderate to severe CMT disease can be helped with surgery. Surgery may be beneficial for severe bone deformities, especially for high arch and hammer toe deformities and Clawed toes can be straightened, high arched feet can be flattened, and unstable ankles can be tightened.

By Disease Type:

On the basis of disease type, the China’s Charcot-Marie-Tooth disease (CMT) therapeutics market can be segmented into CMT-1, CMT-2, CMT-3, CMT-4, CMTX1. CMT-1 is the most common type and it represents 70% of cases.

Fig- Genetic spectrum of CMT among the Han Chinese population in Taiwan. (A) The common genetic causes, and (B) rare genetic causes.


Major Players

Some of the key players in China’s Charcot-Marie-Tooth disease (CMT) therapeutics market are Pharnext; Tasly Pharmaceutical Group Co., Ltd (Shanghai).

Key players are adopting strategies such as mergers and acquisitions, partnerships and licensing agreements. For instance, a licensing agreement between Pharnext and Tasly Pharmaceutical for the development and commercialization of the drug candidate PXT3003 for Charcot-Marie-Tooth type 1A disease in the Chinese market.

The French biopharmaceutical company Pharnext recently announced that its candidate for the treatment of Charcot-Marie-Tooth disease type 1A (CMT1A) was granted priority review by the China Food and Drug Administration (CFDA). Pharnext does not have its direct presence in China, however it made a collaboration with Tasly Pharmaceutical for commercialization of drug PXT3003 in China.

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

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The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

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