China Batten’s Disease (CLN-2) Therapeutics Market


  • Type: Rare Disease Area
  • Published : April 2021
  • Region: Asia
  • Country: China
  • Report ID : 1595

  • Format: PPT, PDF

China Batten’s Disease (CLN-2) Therapeutics Market: Segmented by Therapy (Occupational, Physical, Enzyme Replacement Therapy and Gene Therapy), Drug Type (Cerliponase Alfa, Valproic Acid and Levetiracetam) – Size, Share, Growth, Trends, and Forecasts (2020 – 2028)

SKU: 1595 Categories: ,

Report Overview

China Batten’s Disease (CLN-2) Therapeutics market size stood at around USD xx billion in 2020 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

Batten disease, also known as neuronal ceroid lipofuscinosis, refers to a group of rare inherited neurological conditions that can cause vision loss, progressive motor and cognitive decline, and seizures. The global prevalence of the Batten’s disease is estimated to be 1 to 2 of every 100,000 persons. Juvenile Batten disease occurs in children between ages five and 10. These patients usually live until their late teens or early 20s.

Market Drivers

China is a growing market for batten’s disease (CLN-2) due to increase in research and development, introduction of novel disease therapies, rise in demand for effective therapies among patients and upsurge in global prevalence (1-2 per 100,000 persons) of the disease are projected to fuel the growth of the batten disease market during the forecast period.

However, there are some restraining factors for growth of battens disease therapeutics market in China such as overall high cost of treatment and lack of novel treatment methods.

1. China Batten’s Disease (CLN-2) Therapeutics Market Overview………………….
A. Market Size
2. Market Growth Drivers………………………………………………………………………
A. Increasing Prevalence of Neurological Disorders
B. Rising Need for The Better Treatment Methods
C. Increase in R&D Activities
3. Types of Batten’s Disease (CLN-2) …………………………………………………………….
A. Congenital NCL
B. Infantile NCL
C. Late infantile NCL
D. Juvenile NCL
E. Adult NCL
4. Batten’s Disease (CLN-2) Therapeutics Market Segmentation…………………
A. By Therapy
I. Occupational Therapy
II. Physical Therapy
III. Enzyme Replacement Therapy
IV. Gene Therapy
B. By Drug Type
I. Cerliponase Alfa
II. Valproic Acid
III. Levetiracetam
5. Batten’s Disease (CLN-2) Major Products Market Share…………………………
A. Market Analysis, Insights and Forecast – By Revenue Type
6. Competitive Landscape………………………………………………………………………
A. Major Players
B. Products in Pipeline
7. Key Company Profiles………………………………………………………………………
A. BioMarin Company Overview, Product & Services, Strategies & Financials
B. Amicus Company Overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape……………………………………….
A. Policy Changes and Reimbursement Scenario
9. Factors Driving Future Growth……………………………………………………………
A. New Trends and Development of Batten’s Disease (CLN-2) Therapeutics Market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Therapy:

On the basis of therapy, the China Batten’s disease (CLN-2) therapeutics market can be segmented into occupational therapy, physical therapy, enzyme replacement therapy and gene therapy.

The innovative therapies such as gene therapy and enzyme replacement therapy are used for the treatment of the Batten’s disease.

Occupational therapists are able to help patients improve their fine motor skills and coordination, and maintain their dexterity through training exercises. These exercises work on strengthening hands, wrists, and fingers so that patients are able to develop better hand grip and control.

By Drug Type:

On the basis of drug type, the China Batten’s disease (CLN-2) therapeutics market can be segmented into Cerliponase alfa, Valproic acid and Levetiracetam. Other anti-seizures drugs are used for treatment. These drugs are used to control the symptoms associated with the batten’s disease (symptomatic treatment).


Major Players

Some of the key players in China Batten’s Disease (CLN-2) therapeutics market are BioMarin Pharmaceutical Inc; Amicus Therapeutics Inc; Merck KGaA (acquired Calporta Therapeutics)

The U.S. Food and Drug Administration approved Brineura (cerliponase alfa) as a treatment for a specific form of Batten’s disease. BioMarin company has its presence in China. Although the Brineura product is not approved in China.

Amicus Therapeutics is working on gene therapy for the treatment of Batten’s disease. It announced positive clinical trial data for the Batten’s disease gene therapy. The company does not have its direct presence in China, but it has manufacturing partnership with WuXi Biologics for rare diseases in China.

Calporta/Merck is working on investigational new drug preparation for Batten’s disease. Calporta Therapeutics has been acquired by Merck Group. Merck has its presence in China.

Research Methodology

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  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

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The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

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