Australia Sarcoglynacopathies Market Analysis


  • Type: Rare Disease Area
  • Published : April 2021
  • Region: APAC
  • Country: Australia
  • Report ID : 4090

  • Format: PPT, PDF

Australian Sarcoglycanopathies Therapeutics Market: Segmented by Drug Class (Corticosteroids, Prednisone & Others), and by Distribution Channel (Hospitals, Speciality Clinics & Others) – Growth, Trends, and Forecasts (2020 – 2028F)

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Report Overview

The Australian Sarcoglycanopathies Therapeutics Market size stood at around USD XX billion in 2020 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

Limb-girdle muscular dystrophies (LGMD) are a group of rare progressive genetic disorders that are characterized by wasting (atrophy) and weakness of the voluntary muscles of the hip and shoulder areas (limb-girdle area). These forms of LGMD may range from a severe form often with childhood onset to a mild form often with adult onset. The severity varies greatly even among individuals of the same family. Early onset forms may cause progressive muscle weakness of the legs, hips, abdomen, and shoulder. The progression of muscle weakness of the Sarcoglycanopathies is often more rapid than with other forms of LGMD and affected individuals may need a wheelchair between 12-16 years of age. Individuals with later onset usually experience a slower progression and more mild symptoms. Such individuals usually retain the ability to walk independently late into adulthood. Additional symptoms are often associated with the Sarcoglycanopathies including overgrowth of the calf and tongue muscles, cardiomyopathy, respiratory abnormalities, contractures, and scoliosis.

Market Drivers

Increasing incidence of Sarcoglycanopathies Syndrome, rising health care industries, and increase in government investment to develop health care infrastructure also drive the market growth.

However, rising treatment costs and a lack of awareness among patients and physicians about Sarcoglycanopathies are among the major factors acting as restraints, and will continue to pose a challenge to the Sarcoglycanopathies Therapeutics market in the forecast period.

1. Australian Sarcoglycanopathies Therapeutics Market Overview………………
A. Market Size
2. Market Growth Drivers……………….…………………………………………………….
A. Adoption of Inorganic Growth Strategies
B. Improvement in Healthcare Infrastructure
C. Increase in Awareness Levels of Rare Diseases
3. Major Sarcoglycanopathies Types……………………………………………………….
A. Autosomal Dominant
B. Autosomal Recessive
4. Australian Sarcoglycanopathies Therapeutics Market Segmentation……..
A. By Drug Class
I. Corticosteroids
II. Prednisone
III. Others
B. By Distribution Channel
I. Hospitals
II. Speciality Clinics
III. Others
5. Australian Sarcoglycanopathies Major Products Market Share……………
A. Market Analysis, Insights and Forecast – By Revenue Type
6. Competitive Landscape…………………………………………………………………….
A. Major Players
B. Products in Pipeline
7. Key Company Profiles…………………………………………………………….……….
A. Biomarin Company overview, Product & Services, Strategies & Financials
B. Sarepta Company overview, Product & Services, Strategies & Financials
C. Aspen Pharmacure Company overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape………………………………………
A. Policy changes and Reimbursement scenario
9. Factors Driving Future Growth……………………………………………………………
A. New Trends and Development of Sarcoglycanopathies Therapeutics market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Drug Class:

On the basis of drug class, Sarcoglycanopathies Therapeutics market is segmented into Corticosteroids, Predisone and others. Corticosteroids are likely to emerge as the top-selling products. Various scientific research has found that compared to various products to treat Sarcoglycanopathies, corticosteroids help in improving muscle strength for up to two to five years, however, long-term benefit of corticosteroids is still not clear.

By Distribution Channel:

On the basis of distribution channel, Sarcoglycanopathies Therapeutics market is segmented into Hospitals, Speciality clinics & others. Hospital pharmacies are likely to be the largest distribution channel between 2020 and 2028. Increasing number of people are being hospitalized for Sarcoglycanopathies. Hence, drugs for Sarcoglycanopathies are being sold on a large scale through hospital pharmacies.

Top Major Players

Inorganic growth strategies activities witnessed in the market were acquisitions and partnership & collaborations. These activities have paved way for expansion of business and customer base of market players. Major players operating in the market include BioMarin Pharmaceutical Australia Pty Ltd., Sarepta Therapeutics Inc., & Aspen Pharmacare Australia Pty Ltd.

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision making for business stakeholders. Our focused approach to develop reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

Our analysis methodology involves three critical stages:

Stage I: Market Data Collection

Primary Interviews: We have developed a network of experts, freelancers and researchers across countries through which we engage with local experts to gather key data points and assumptions around each market. We also engage regularly with some of the best market research agencies such as Atheneum, GuidePoint, GLG, etc. to conduct surveys and interviews, and build intelligence. We have language translators as a part of our team, who between them can cover 30+ languages allowing us to extract better local insights.

Secondary Data Collection: We have developed strong expertise and experience in secondary data collection methods for developing unique data sets and research material. We gather data from multiple reliable sources to maintain the high level of accuracy and consistency. The market data is analysed and forecasted using appropriate statistical and coherent models. The report offers an overall analysis of the market size, growth, market share as well as segment-level analysis of the specific market. Our report includes precise, to the point information related to the overall market, competition, growth drivers, challenges, regulatory updates, and competition.

Data Sources: We have access to multiple highly reliable free and subscription data sources. We have many years of experience to understand which sources are more dependable for what and which to prefer for the reliable and latest information. The key sources of information include the following, but are not limited to:

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Stage II: Market Data Analysis and Statistical Model

Market Trends: We generally look at macro parameter and micro indicators. The macro parameters includes changes in government policies, demand and supply of the market, government intervention programs and major market share. The micro indicators GDP growth, market size, market volume etc. We also understand nuances specific to each country like US, Canada, India, Germany, etc. and have worked across 60+ countries and hence no only understand global trends, but how these differ by country, how payment models, market structure, cultural parameters, etc. differ in each country.

Market Sizing and Analysis: Our expert data analytics team has created various market forecast models by employing the top-down approach i.e. start with large overall market and segment different areas and bottom-up approach i.e. start with population and epidemiology and roll up based on spend, etc., estimating the size of the market, and distributing among the geographic and/or product segments.

The top-down approach mainly used for new product forecasting and bottom-up approach is used for demand estimation of any product for different countries summed up to form total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

Data Triangulation & Validation:

Data triangulation of various sources and results of the research are carried out by benchmarking with reliable sources such as industry statistics, statistical databases and the company level averages etc.

We make sure to finalize the numbers in alignment to the market research. Firstly, our internal experts ensure thorough validation and checking to ensure the accurate and precise analysis and then validation is also done using multiple data analysis model.  Two level validation is done and entails finalization of report scope and to way of representation pattern.

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analysed and synthesized. A second series of interviews are done if necessary to check and validate. The future opportunities are analysed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results are then, interpreted by considering following parameters: (a partial list)

  • Establishing market drivers and trends
  • Analyzing regulatory landscape to understand future growth
  • Market Segment based analysis to obtain revenue / volume
  • Analyzing current needs and determining penetration to estimate market

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Data curated from the analysis and interpretation are drawn to portray all in one consolidated report.

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The foreign exchange rates are calculated on the respective dates and for the respective regions covered in the study.

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