Australia MPS VI Market Analysis

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  • Type: Rare Disease Area
  • Published : April 2021
  • Region: APAC
  • Country: Australia
  • Report ID : 4088

  • Format: PPT, PDF

Australian MPS VI Therapeutics Market: Segmented by Treatment (Enzyme Replacement Therapy, Stem Cell Therapy and Other therapies), and by Distribution Channel (Retail Pharmacies, Hospital Pharmacies & Online Pharmacies) – Growth, Trends, and Forecasts (2020 – 2028F)

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Report Overview

The Australian MPS VI Therapeutics Market size stood at around USD XX billion in 2020 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

MPS VI is an inherited disorder that encompasses a wide spectrum of severity. Physical symptoms may include bone and joint malformation, hearing and vision problems, and heart and breathing difficulties. The rate of disease progression and age of onset vary considerably, even in affected siblings: in some, it may be rapid with diagnosis in the first few years of life; in others it may be relatively slow and diagnosis may not occur until the third or fourth decade. Generally, if clinical symptoms are apparent early in life it is more likely that disease progress will be more rapid. MPS VI is also known as Maroteaux-Lamy syndrome. Mucopolysaccharides are used by the cells to build connective tissues in the body, such as skin, muscle, cartilage and bone. They also help with many other cellular functions, including growth control, organ development and signalling between cells. n people with an MPS disorder one of the lysosomal enzymes that is needed to degrade mucopolysaccharides is either missing or is present at levels that do not allow the recycling process to work properly.

It has been estimated that in Australia about 1 in 248,372 births are affected by MPS VI. The incidence of all MPS disorders combined (of which 11 are currently recognised) is estimated to be 1 in 25,000 births.

Market Drivers

The growth in the number of products in the preliminary and advanced stages of R&D along with the focus on treatment of rare diseases is anticipated to drive the growth in the market at a considerably fast rate. With the approval of the elosulfase alpha (VIMIZIM), the market is expected to be boosted several products currently in the pipeline of various companies can be anticipated to undergo regulatory approvals for the marketing, if they have favourable clinical trials results.  However, rising treatment costs and a lack of awareness among patients and physicians about MPS VI are among the major factors acting as restraints, and will continue to pose a challenge to the MPS VI treatment market in the forecast period.

1. Australian MPS VI Therapeutics Market Overview……………………………………….
A. Market Size
2. Market Growth Drivers………………..…………………………………………………..
A. Adoption of Inorganic Growth Strategy
B. Increase in Awareness Levels of Rare Diseases
3. Major MPS VI Types……………………………………………………………………….
A. Macrocephaly
B. Hydrocephalus
C. Others
4. Australian MPS VI Therapeutics Market Segmentation………………………………..
A. By Treatment Class
I. Enzyme Replacement Therapy
II. Stem Cell Therapy
III. Other Therapies
B. By Distribution Channels
I. Retail Pharmacies
II. Hospital Pharmacies
III. Online Pharmacies
5. Australian MPS VI Major Products Market Share……………………………………
A. Market Analysis, Insights and Forecast – By Revenue Type
6. Competitive Landscape…………………………………………………………………..
A. Major Players
B. Products in Pipeline
7. Key Company Profiles…………………………………………………………………….
A. BioMarin Company overview, Product & Services, Strategies & Financials
B. Ultragenyx Benckiser Company overview, Product & Services, Strategies & Financials
C. Takeda Company overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape……………………………………..
A. Policy changes and Reimbursement scenario
9. Factors Driving Future Growth………………………………………………………….
A. New Trends and Development of MPS VI Therapeutics market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Treatment:

On the basis of treatment, the MPS VI Therapeutics market is segmented into enzyme replacement therapy, stem cell therapy & other therapies. At present, enzyme replacement therapy accounts for the largest proportion of the market and the trend are expected to remain same during the forecast period.

By Distribution Channels:

In terms of distribution channel, MPS VI Therapeutics market have been segmented into hospital pharmacies, retail pharmacies, and online pharmacies. Hospitals have amassed most share of the market due to their widespread presence and the preference for hospitals among patients.

Top 5 Major Players

The market players from Mucopolysaccharidosis VI Therapeutics market are anticipated to have lucrative growth opportunities in the future with the rising demand for Mucopolysaccharidosis Treatment in the market. Major players operating in the market include BioMarin Pharmaceutical Australia Pty Ltd., Ultragenyx Pharmaceutical Inc., Takeda Pharmaceutical Company Limited., Abeona Therapeutics Inc., & Eloxx Pharmaceuticals.

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision making for business stakeholders. Our focused approach to develop reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

Our analysis methodology involves three critical stages:

Stage I: Market Data Collection

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Market Sizing and Analysis: Our expert data analytics team has created various market forecast models by employing the top-down approach i.e. start with large overall market and segment different areas and bottom-up approach i.e. start with population and epidemiology and roll up based on spend, etc., estimating the size of the market, and distributing among the geographic and/or product segments.

The top-down approach mainly used for new product forecasting and bottom-up approach is used for demand estimation of any product for different countries summed up to form total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

Data Triangulation & Validation:

Data triangulation of various sources and results of the research are carried out by benchmarking with reliable sources such as industry statistics, statistical databases and the company level averages etc.

We make sure to finalize the numbers in alignment to the market research. Firstly, our internal experts ensure thorough validation and checking to ensure the accurate and precise analysis and then validation is also done using multiple data analysis model.  Two level validation is done and entails finalization of report scope and to way of representation pattern.

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analysed and synthesized. A second series of interviews are done if necessary to check and validate. The future opportunities are analysed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results are then, interpreted by considering following parameters: (a partial list)

  • Establishing market drivers and trends
  • Analyzing regulatory landscape to understand future growth
  • Market Segment based analysis to obtain revenue / volume
  • Analyzing current needs and determining penetration to estimate market

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Data curated from the analysis and interpretation are drawn to portray all in one consolidated report.

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The foreign exchange rates are calculated on the respective dates and for the respective regions covered in the study.

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