Australia Fabry Disease Market Analysis


  • Type: Rare Disease Area
  • Published : April 2021
  • Region: APAC
  • Country: Australia
  • Report ID : 4080

  • Format: PPT, PDF

Australian Fabry Disease Therapeutics Market: Segmented by Diagnosis, by Treatment, and by End Users – Size, Share, Impact, Growth, Trends, and Forecasts (2020 – 2028F)

SKU: 4080 Categories: ,

Report Overview

The Australian Fabry Disease Therapeutics Market size stood at around USD xx billion in 2020 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

Fabry Disease (also known as Anderson-Fabry Disease) is a rare genetic disorder which is caused by the deficiency of defective gene i.e., alpha-galactosidase-A gene (GLA gene) which leads to deficiency of an alpha-galactosidase enzyme. Alpha-galactosidase A (AGA) enzyme hydrolyses the terminal a -galactosyl moieties from glycolipids and glycoproteins. This disease is caused by an abnormal build-up of a specific fatty matter called globotriaosylceramide in multiple tissues of the body including eyes, skin, kidney, gastrointestinal system, brain, heart, and central nervous system.

People probably carry from 5 to 10 genes with mutations in each of their cells. It has been estimated that Fabry disease affects between 1:40,000 people, in males it is around 1:17,000. Fabry is seen across all ethnic groups. In a research, the average age of 44.5 years of Fabry affected patients has been reported while 81% of women and 61% of men has been found the classical Fabry disease.

Market Drivers

Growing prevalence of Fabry Disease and its consequences on healthcare expenditure have augmented the demand for special treatments, positively impacting the Fabry Disease treatment market growth during the forecast period. The increasing focus on research activities and development of novel therapeutic drugs has uplifted the Fabry Disease therapeutics market value. Moreover, favourable government policies aiming at creating awareness pertaining to the Fabry disease treatment is leading to increased adoption of effective treatments of Fabry disease during the forecast period. However, there are several factors hindering the efficient and effective clinical trials of drug development of Fabry disease including low patient numbers, limited understanding of pathology and progression, and lack of established endpoints.

Fabry Disease Types:

Based on type, the Fabry Disease market can be segmented into type-1, type-2 and others. Among all, the maximum patients are identified being suffered from the type-2 Fabry disease, so the type-2 Fabry disease is anticipated to acquire a major market share during the forecast period.

1. Australian Fabry Disease Therapeutics Market Overview……………………….
A. Market Size
2. Market Growth Drivers………………………….…………………………………………………….…
A. Rising Prevalence of Fabry Disease
B. Financial Support to the Researchers for Developing Novel Intervention
3. Major Types of Fabry Disease………………………………………………………………………………….
A. Type-1 Classic Phenotype
B. Type-2 Later-onset Phenotype
4. Fabry Disease Therapeutics Market Segmentation…………………………………..
A. By Diagnosis
I. Blood Test
II. Urine Test
III. Thyroid Test
IV. Lung Function Test
V. Hearing and Eye Examination
VI. Imaging Techniques
B. By Treatment
I. Enzyme Replacement Therapy (ERP)
II. Chaperone Therapy
III. Gene Therapy
IV. Analgesics
V. Anticonvulsants
VI. Non-steroidal Anti-inflammatory Drugs (NSAIDs)
VII. Others
C. By End Users
I. Hospitals and Clinics
II. Diagnostic Centres
III. Research and Academic Institutes
IV. Others
5. Fabry Disease Major Products Market Share……………………………………………
A. Market Analysis, Insights and Forecast – By Revenue Type
6. Competitive Landscape…………………………………………………………………………..
A. Major Players
B. Products in Pipeline
7. Key Company Profiles………………………………………………………………………………
A. Sanofi Company overview, Product & Services, Strategies & Financials
B. Amicus Company overview, Product & Services, Strategies & Financials
C. Takeda Company overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape……………………………………
A. Policy changes and Reimbursement scenario
9. Factors Driving Future Growth………………………………………………………………..
A. New Trends and Development of Fabry Disease Therapeutics Market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Diagnosis:

The diagnosis of Fabry Disease Therapeutics market can be segmented into blood test, urine test, thyroid test, lung function test, hearing and eye examination and imaging techniques. The imaging segment is further segmented into Echocardiogram, Electrocardiogram (EKG), Brain MRI, CT scan and others.

By Treatment:

On the basis of treatment, the Fabry Disease Therapeutics market can be divided into an enzyme replacement therapy (ERT), chaperone therapy, gene therapy, analgesics, anticonvulsants, NSAIDs and others. ERT is a long-term therapy whereby the missing or deficient enzyme is given via an intravenous infusion. Currently Fabrazyme (agalsidase beta) and Replagal (agalsidase alpha) are both are approved ERTs treatment of Fabry disease in the Australia. ERT helps to normalise kidney and heart function, and blood supply to the brain. With respect to chaperone therapy, Galafold (migalastat), is an oral capsule taken every other day and has been available in the Australia. Strong sales of Fabrazyme and Replagal and potential approval of promising pipeline candidates are supporting the dominance of the ERT segment during the forecast period.

By End Users:

Based on the end user, the Fabry Disease Therapeutics market has been segmented into hospitals & clinics, diagnostic centres, research & academic institutes, and others. In Australia, mostly patients have accessed the Fabry disease treatment in hospitals. Thus, the hospitals segment commands the largest market share in terms of value during the forecast period.

Top Major Players

The major key players operating in Australia Fabry Disease Therapeutics market are Sanofi- Aventis, Amicus Therapeutics, Amgen Inc, and Takeda Pharmaceuticals prevailing in the Australian market during the forecast period. Fabrazyme, Replagal, and Galafold are most commonly used to treat Fabry disease in Australia.

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision making for business stakeholders. Our focused approach to develop reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

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The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

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We make sure to finalize the numbers in alignment to the market research. Firstly, our internal experts ensure thorough validation and checking to ensure the accurate and precise analysis and then validation is also done using multiple data analysis model.  Two level validation is done and entails finalization of report scope and to way of representation pattern.

Stage III: Interpretation and Presentation

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