Australia Fabry Disease Market Analysis

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  • Type: Rare Disease Area
  • Published : April 2021
  • Region: APAC
  • Country: Australia
  • Report ID : 4080

  • Format: PPT, PDF

Australian Fabry Disease Therapeutics Market: Segmented by Diagnosis, by Treatment, and by End Users – Size, Share, Impact, Growth, Trends, and Forecasts (2020 – 2028F)

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Report Overview

The Australian Fabry Disease Therapeutics Market size stood at around USD xx billion in 2020 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

Fabry Disease (also known as Anderson-Fabry Disease) is a rare genetic disorder which is caused by the deficiency of defective gene i.e., alpha-galactosidase-A gene (GLA gene) which leads to deficiency of an alpha-galactosidase enzyme. Alpha-galactosidase A (AGA) enzyme hydrolyses the terminal a -galactosyl moieties from glycolipids and glycoproteins. This disease is caused by an abnormal build-up of a specific fatty matter called globotriaosylceramide in multiple tissues of the body including eyes, skin, kidney, gastrointestinal system, brain, heart, and central nervous system.

People probably carry from 5 to 10 genes with mutations in each of their cells. It has been estimated that Fabry disease affects between 1:40,000 people, in males it is around 1:17,000. Fabry is seen across all ethnic groups. In a research, the average age of 44.5 years of Fabry affected patients has been reported while 81% of women and 61% of men has been found the classical Fabry disease.

Market Drivers

Growing prevalence of Fabry Disease and its consequences on healthcare expenditure have augmented the demand for special treatments, positively impacting the Fabry Disease treatment market growth during the forecast period. The increasing focus on research activities and development of novel therapeutic drugs has uplifted the Fabry Disease therapeutics market value. Moreover, favourable government policies aiming at creating awareness pertaining to the Fabry disease treatment is leading to increased adoption of effective treatments of Fabry disease during the forecast period. However, there are several factors hindering the efficient and effective clinical trials of drug development of Fabry disease including low patient numbers, limited understanding of pathology and progression, and lack of established endpoints.

Fabry Disease Types:

Based on type, the Fabry Disease market can be segmented into type-1, type-2 and others. Among all, the maximum patients are identified being suffered from the type-2 Fabry disease, so the type-2 Fabry disease is anticipated to acquire a major market share during the forecast period.

1. Australian Fabry Disease Therapeutics Market Overview……………………….
A. Market Size
2. Market Growth Drivers………………………….…………………………………………………….…
A. Rising Prevalence of Fabry Disease
B. Financial Support to the Researchers for Developing Novel Intervention
3. Major Types of Fabry Disease………………………………………………………………………………….
A. Type-1 Classic Phenotype
B. Type-2 Later-onset Phenotype
4. Fabry Disease Therapeutics Market Segmentation…………………………………..
A. By Diagnosis
I. Blood Test
II. Urine Test
III. Thyroid Test
IV. Lung Function Test
V. Hearing and Eye Examination
VI. Imaging Techniques
B. By Treatment
I. Enzyme Replacement Therapy (ERP)
II. Chaperone Therapy
III. Gene Therapy
IV. Analgesics
V. Anticonvulsants
VI. Non-steroidal Anti-inflammatory Drugs (NSAIDs)
VII. Others
C. By End Users
I. Hospitals and Clinics
II. Diagnostic Centres
III. Research and Academic Institutes
IV. Others
5. Fabry Disease Major Products Market Share……………………………………………
A. Market Analysis, Insights and Forecast – By Revenue Type
6. Competitive Landscape…………………………………………………………………………..
A. Major Players
B. Products in Pipeline
7. Key Company Profiles………………………………………………………………………………
A. Sanofi Company overview, Product & Services, Strategies & Financials
B. Amicus Company overview, Product & Services, Strategies & Financials
C. Takeda Company overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape……………………………………
A. Policy changes and Reimbursement scenario
9. Factors Driving Future Growth………………………………………………………………..
A. New Trends and Development of Fabry Disease Therapeutics Market
B. Future Opportunities
10. Conclusion

Market Segmentation

By Diagnosis:

The diagnosis of Fabry Disease Therapeutics market can be segmented into blood test, urine test, thyroid test, lung function test, hearing and eye examination and imaging techniques. The imaging segment is further segmented into Echocardiogram, Electrocardiogram (EKG), Brain MRI, CT scan and others.

By Treatment:

On the basis of treatment, the Fabry Disease Therapeutics market can be divided into an enzyme replacement therapy (ERT), chaperone therapy, gene therapy, analgesics, anticonvulsants, NSAIDs and others. ERT is a long-term therapy whereby the missing or deficient enzyme is given via an intravenous infusion. Currently Fabrazyme (agalsidase beta) and Replagal (agalsidase alpha) are both are approved ERTs treatment of Fabry disease in the Australia. ERT helps to normalise kidney and heart function, and blood supply to the brain. With respect to chaperone therapy, Galafold (migalastat), is an oral capsule taken every other day and has been available in the Australia. Strong sales of Fabrazyme and Replagal and potential approval of promising pipeline candidates are supporting the dominance of the ERT segment during the forecast period.

By End Users:

Based on the end user, the Fabry Disease Therapeutics market has been segmented into hospitals & clinics, diagnostic centres, research & academic institutes, and others. In Australia, mostly patients have accessed the Fabry disease treatment in hospitals. Thus, the hospitals segment commands the largest market share in terms of value during the forecast period.

Top Major Players

The major key players operating in Australia Fabry Disease Therapeutics market are Sanofi- Aventis, Amicus Therapeutics, Amgen Inc, and Takeda Pharmaceuticals prevailing in the Australian market during the forecast period. Fabrazyme, Replagal, and Galafold are most commonly used to treat Fabry disease in Australia.

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

Based on our many years of experience, we believe that these are the parameters that are critical to decision making for business stakeholders. Our focused approach to develop reports focused on 10 key parameters, enabled us to arrive at the name “Insights10”.

Our analysis methodology involves three critical stages:

Stage I: Market Data Collection

Primary Interviews: We have developed a network of experts, freelancers and researchers across countries through which we engage with local experts to gather key data points and assumptions around each market. We also engage regularly with some of the best market research agencies such as Atheneum, GuidePoint, GLG, etc. to conduct surveys and interviews, and build intelligence. We have language translators as a part of our team, who between them can cover 30+ languages allowing us to extract better local insights.

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Data Sources: We have access to multiple highly reliable free and subscription data sources. We have many years of experience to understand which sources are more dependable for what and which to prefer for the reliable and latest information. The key sources of information include the following, but are not limited to:

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Market Trends: We generally look at macro parameter and micro indicators. The macro parameters includes changes in government policies, demand and supply of the market, government intervention programs and major market share. The micro indicators GDP growth, market size, market volume etc. We also understand nuances specific to each country like US, Canada, India, Germany, etc. and have worked across 60+ countries and hence no only understand global trends, but how these differ by country, how payment models, market structure, cultural parameters, etc. differ in each country.

Market Sizing and Analysis: Our expert data analytics team has created various market forecast models by employing the top-down approach i.e. start with large overall market and segment different areas and bottom-up approach i.e. start with population and epidemiology and roll up based on spend, etc., estimating the size of the market, and distributing among the geographic and/or product segments.

The top-down approach mainly used for new product forecasting and bottom-up approach is used for demand estimation of any product for different countries summed up to form total market. We are able to round off insights and build stronger forecasts because we always do both these methods and triangulate the final numbers.

The study on the market covers the analysis of the leading geographies such as North America, Europe, Asia-Pacific, and Africa for the period of 2020 to 2028. The qualitative analysis covers the industry landscape and trends, market opportunities, competitive landscape and policy and regulatory scenario and the quantitative analysis covers different market estimates and forecasts.

Data Triangulation & Validation:

Data triangulation of various sources and results of the research are carried out by benchmarking with reliable sources such as industry statistics, statistical databases and the company level averages etc.

We make sure to finalize the numbers in alignment to the market research. Firstly, our internal experts ensure thorough validation and checking to ensure the accurate and precise analysis and then validation is also done using multiple data analysis model.  Two level validation is done and entails finalization of report scope and to way of representation pattern.

Stage III: Interpretation and Presentation

Analysis & Interpretation: The information gathered is then analysed and synthesized. A second series of interviews are done if necessary to check and validate. The future opportunities are analysed by understanding product commercialization and many other factors. It also comprises the analysis of data discrepancies observed across various data sources. Information procured from secondary and primary results are then, interpreted by considering following parameters: (a partial list)

  • Establishing market drivers and trends
  • Analyzing regulatory landscape to understand future growth
  • Market Segment based analysis to obtain revenue / volume
  • Analyzing current needs and determining penetration to estimate market

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Data curated from the analysis and interpretation are drawn to portray all in one consolidated report.

Presentation & Reporting: The market research report is presented in different forms such as charts by using a scientific approach for easy understanding. Historic, current and future analysis is provided for each market in terms of both value and volume. The size of the market is interpreted in the US Dollar value and the respective unit, based on the product, for volume consumptions.
The foreign exchange rates are calculated on the respective dates and for the respective regions covered in the study.

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