Australia Angelman Syndrome Market Analysis


  • Type: Rare Disease Area
  • Published : April 2021
  • Region: APAC
  • Country: Australia
  • Report ID : 4094

  • Format: PPT, PDF

Australian Angelman Syndrome Therapeutics Market: Segmented by Treatment (Anticonvulsants, Ankle braces/supports, Physical therapy, Speech therapy, Occupational therapy, Behavioral modification therapy, Use of communication devices, and other therapies), and Distribution Channel (Hospitals, Speciality Clinics & Others) – Growth, Trends, and Forecasts (2020 – 2028)

SKU: 4094 Categories: ,

The Australian Angelman Syndrome Therapeutics market size stood at around USD XX billion in 2020 and is projected to reach USD xx billion by 2028, exhibiting a CAGR of xx% during the forecast period.

Angelman syndrome is a rare genetic and neurological disorder characterized by severe developmental delay and learning disabilities; absence or near absence of speech; inability to coordinate voluntary movements (ataxia); tremulousness with jerky movements of the arms and legs and a distinct behavioral pattern characterized by a happy disposition and unprovoked episodes of laughter and smiling. Although those with the syndrome may be unable to speak, many gradually learn to communicate through other means such as gesturing.

In Australia, Angelman syndrome affects males and females in equal numbers. The prevalence of Angelman syndrome is estimated to be out of the whole population, people affected by Angelman syndrome are 1,659. Angelman syndrome is not a degenerative disease. Children with Angelman syndrome can expect a normal lifespan.

Market Growth Drivers

Angelman syndrome treatment market is expected to grow over the forecast period, due to increasing research activities and R&D expenditure (for instance FAST Australia has raised over two million dollars of which $1.5 million has been invested in research and education. They have held three conferences with researchers and experts from within Australia and globally). Government initiatives in developing new treatment options for Angelman syndrome are expected to drive the growth of the Australian Angelman syndrome treatment market over the forecast period 2020-2028. Furthermore, the effectiveness of the treatment by reducing the effect of the symptoms is also driving the growth of the Australian Angelman syndrome treatment market. Improvements in the healthcare sector are further facilitating the growth of the Angelman syndrome treatment market.

However, rising treatment costs and lack of awareness among patients and physicians & low diagnosis rate because of difficulty in diagnosis about Angelman Syndrome are among the major factors acting as restraints in the forecast period.

1. Australian Angelman Syndrome Therapeutics Market Overview……………………
A. Market Size
2. Market Growth Drivers & Restraints…………………………………………………….
A. Increased R & D expenditure
B. Increase in Awareness Levels of Rare Diseases
C. High Treatment Costs
D. Low Diagnosis rates
3. Major Angelman Syndrome Types………………………………………………………
A. Genetic
B. Acquired by Chance
4. Australian Angelman Syndrome Therapeutics Market Segmentation……………….
A. By Treatment
I. Anticonvulsants
II. Ankle braces/supports
III. Physical therapy
IV. Speech therapy
V. Occupational therapy
VI. Behavioral modification therapy
VII. Use of communication devices
VIII. Other Therapies
B. By Distribution Channel
I. Hospitals
II. Speciality Clinics
III. Others
5. Australian Angelman Syndrome Major Products Market Share……………………
A. Market Analysis, Insights and Forecast – By Revenue Type
6. Competitive Landscape…………………………………………………………………
A. Major Players
B. Products in Pipeline
7. Key Company Profiles…………………………………………………………………..
A. Cipla Company overview, Product & Services, Strategies & Financials
B. Roche Company overview, Product & Services, Strategies & Financials
C. Sanofi- Aventis Company overview, Product & Services, Strategies & Financials
8. Healthcare Policies and Regulatory Landscape……………………………………
A. Policy changes and Reimbursement scenario
9. Factors Driving Future Growth…………………………………………………………
A. New Trends and Development of Angelman Syndrome Therapeutics Market
B. Future Opportunities
10. Conclusion

By Treatment:

On the basis of treatment, the Angelman Syndrome Therapeutics market can be segmented into anticonvulsants, ankle braces/supports, physical therapy, speech therapy, occupational therapy, behavioral modification therapy, use of communication devices, and other therapies. Therapies for Angelman syndrome are symptomatic and supportive & there is no genetic therapy or curative medication available. Anti-seizure medications are helpful to those experiencing seizures & usually seizures can be adequately controlled with a single medication. Ankle braces/supports and physical therapy can help in the achievement of walking. Most children with Angelman syndrome benefit from physical, speech, and occupational therapy. Behavioral modification therapy may be used to discourage unwanted behaviors. The use of special communication devices such as computer picture-based systems, voice emitting devices and other modern uses of technology all help Angelman syndrome individuals provide for improved learning and social communication.

By Distribution Channel:

On the basis of distribution channels, the Angelman Syndrome Therapeutics market can be bifurcated into hospital pharmacies, retail pharmacies, and online pharmacies. Hospitals are likely to be the largest distribution channel between 2020 and 2028. An increasing number of people are being hospitalized for Angelman Syndrome. Hence, drugs for Angelman Syndrome are being sold on a large scale through hospitals.

Top Major Players

Various companies are focusing on organic growth strategies such as product launches, product approvals, and others such as patents and events. Inorganic growth strategies activities witnessed in the market were acquisitions and partnership & collaborations. These activities have paved the way for the expansion of the business and the customer base of market players. Major players operating in the market include BioMarin Pharmaceutical Australia Pty Ltd., Alphapharm Pty Ltd., Arrow Pharma Pty Ltd., Aspen Pharmacare Australia Pty Ltd., Avallon Pharmaceuticals Pty Ltd., Cipla Australia Pty Ltd., Strides Pharma Science Pty Ltd., Amneal Pharma Australia Pty Ltd., Apotex Pty Ltd., Torrent Australasia Pty Ltd., Sanofi-Aventis Australia Pty Ltd., AFT Pharmaceuticals Pty Ltd., Roche Products Pty Ltd., Orion Laboratories Pty Ltd T/A Perrigo Australia, AdiraMedica Pty Ltd.

Research Methodology

Insights10 will provide you reports within 10 key parameters which are:

  1. Market overview
  2. Market growth drivers & restraints
  3. Epidemiology or disease type
  4. Market segmentation
  5. Market share
  6. Competitive landscape
  7. Key company profiles
  8. Healthcare policies & regulatory framework
  9. Reimbursement scenario
  10. Factors driving future growth

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